New England Journal of Medicine March 19, 2015

Polysaccharide Conjugate Vaccine against Pneumococcal Pneumonia in Adults

Marc J.M. Bonten, Susanne M. Huijts, Marieke Bolkenbaas et al.

Bottom Line

The CAPiTA trial demonstrated that the 13-valent pneumococcal conjugate vaccine (PCV13) effectively prevents first episodes of vaccine-type pneumococcal community-acquired pneumonia and invasive pneumococcal disease in adults aged 65 and older.

Key Findings

1. Vaccine efficacy for preventing first episodes of vaccine-type community-acquired pneumonia (VT-CAP) was 45.6% (49 cases in the PCV13 group vs. 90 cases in the placebo group; 95.2% CI, 21.8 to 62.5).
2. Vaccine efficacy for nonbacteremic and noninvasive VT-CAP was 45.0% (33 cases in the PCV13 group vs. 60 cases in the placebo group; 95.2% CI, 14.2 to 65.3).
3. Vaccine efficacy against vaccine-type invasive pneumococcal disease (VT-IPD) was 75.0% (7 cases in the PCV13 group vs. 28 cases in the placebo group; 95% CI, 41.4 to 90.8).
4. There was no statistically significant reduction in all-cause community-acquired pneumonia, which occurred in 747 persons in the PCV13 group compared to 787 in the placebo group (vaccine efficacy, 5.1%; 95% CI, -5.1 to 14.2).

Study Design

Design
RCT
Double-Blind
Sample
84,496
Patients
Duration
3.97 yr
Median
Setting
Netherlands
Population Immunocompetent adults 65 years of age or older
Intervention A single dose of the 13-valent pneumococcal polysaccharide conjugate vaccine (PCV13)
Comparator A single dose of matched placebo
Outcome First episode of confirmed vaccine-type strains of pneumococcal community-acquired pneumonia (VT-CAP)

Study Limitations

The absolute risk reduction for vaccine-type pneumonia and invasive disease was very small, meaning a large number needed to vaccinate (NNV) to prevent a single event.
The trial failed to demonstrate a significant reduction in all-cause pneumonia or all-cause mortality, reflecting that the vast majority of pneumonia in older adults is caused by non-vaccine serotypes or non-pneumococcal pathogens.
The study was conducted in a country (the Netherlands) without a mature pediatric PCV13 immunization program at the time; thus, the measured absolute benefit was likely higher than it would be in regions with strong, established pediatric PCV13 programs that confer significant indirect herd protection to adults.

Clinical Significance

CAPiTA was a landmark, highly anticipated trial that provided the definitive clinical efficacy data needed to prove that conjugate pneumococcal vaccines could prevent nonbacteremic, mucosal pneumococcal pneumonia in older adults—a benefit that had been historically difficult to establish with the older 23-valent polysaccharide vaccine (PPSV23). These findings directly prompted global guideline updates, including the US ACIP's 2014 recommendation for routine PCV13 administration in all adults 65 years of age and older.

Historical Context

Historically, older adults only received the 23-valent pneumococcal polysaccharide vaccine (PPSV23), which effectively protected against invasive pneumococcal disease but showed inconsistent, heavily debated efficacy against nonbacteremic community-acquired pneumonia. Following the dramatic success of T-cell-dependent conjugate vaccines in children, the CAPiTA trial was designed to evaluate whether PCV13 could close the gap in preventing mucosal disease in the elderly. While the trial was a success, the subsequent widespread use of PCV13 in children induced strong herd immunity, decreasing the residual burden of PCV13-type disease in adults. This indirect effect eventually prompted the ACIP to transition routine PCV13 use in older adults to 'shared clinical decision-making' in 2019, paving the way for the development of newer, broader conjugate vaccines (PCV15 and PCV20).

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

What is the fundamental immunological difference between the 13-valent pneumococcal conjugate vaccine (PCV13) used in the CAPiTA trial and the 23-valent pneumococcal polysaccharide vaccine (PPSV23), and how does this affect memory immunity?

Key Response

PCV13 conjugates polysaccharides to a carrier protein (CRM197), engaging T-helper cells to produce a T-cell-dependent response, leading to mucosal immunity and memory B cells. PPSV23 produces a T-cell-independent response largely driven by B cells without mucosal immunity or robust long-term memory.

Resident
Resident

Based on the conjugate vaccine efficacy demonstrated in the CAPiTA trial, what is the rationale behind sequencing a conjugate pneumococcal vaccine before a polysaccharide vaccine (PPSV23) in vaccine-naive older adults?

Key Response

To maximize the T-cell dependent immune boost before broadening serotype coverage, principles of immunology dictate giving the conjugate vaccine first. This primes the immune system, leading to a stronger, boosted anamnestic response when the polysaccharide vaccine is given at least one year later.

Fellow
Fellow

The CAPiTA trial demonstrated a significant reduction in vaccine-type pneumococcal pneumonia. Why might the overall incidence of community-acquired pneumonia (CAP) in the elderly population remain largely unchanged despite widespread conjugate vaccine administration?

Key Response

This highlights the concepts of serotype replacement and the proportional etiology of CAP. As PCV13 strains are eliminated, non-vaccine pneumococcal serotypes and non-pneumococcal pathogens (such as respiratory viruses or atypical bacteria) fill the ecological niche, keeping the overall all-cause CAP incidence relatively stable.

Attending
Attending

How does the concept of herd immunity from pediatric PCV13 vaccination programs complicate the long-term clinical applicability and cost-effectiveness of the CAPiTA trial findings for adults aged 65 and older?

Key Response

Routine pediatric PCV13 vaccination drastically reduced the circulation of PCV13 strains across all age groups. As the prevalence of these vaccine-type strains dropped in adults, the absolute risk reduction and cost-effectiveness of adult PCV13 vaccination diminished, demonstrating how shifting epidemiology can alter the clinical utility of a previously positive trial.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

The CAPiTA trial utilized a highly specific serotype-specific urinary antigen test (UAT) to define its primary endpoint. What are the statistical and methodological trade-offs of using this assay compared to standard blood and sputum cultures?

Key Response

The UAT increases specificity for vaccine-type pneumonia, reducing misclassification bias that would otherwise dilute the vaccine efficacy estimate towards the null. However, its imperfect sensitivity means many true cases are missed, which lowers the overall captured event rate, reduces statistical power, and potentially underestimates the absolute risk reduction.

Journal Editor
Journal Editor

As a peer reviewer evaluating the CAPiTA manuscript, how would you scrutinize the trial handling of missing data and loss to follow-up over the nearly 4-year study period, particularly regarding informative censoring in a geriatric cohort?

Key Response

Older adults have high morbidity and mortality from competing risks. If subjects dropped out due to declining overall health, making them inherently more susceptible to pneumonia, standard survival analyses might bias the vaccine efficacy estimates. A rigorous review would demand competing risk analyses (e.g., Fine-Gray models) and sensitivity analyses for attrition.

Guideline Committee
Guideline Committee

How did the CAPiTA trial initially prompt the ACIP to recommend PCV13 for all adults 65 and older in 2014, and what epidemiological evidence subsequently led to the 2019 revision retracting this universal recommendation in favor of shared clinical decision-making?

Key Response

CAPiTA provided the Grade A randomized trial evidence for PCV13 efficacy against non-bacteremic pneumonia, prompting the 2014 universal recommendation. By 2019, ACIP analysis revealed that pediatric PCV13 administration had led to such profound herd immunity that the remaining burden of PCV13-type disease in older adults was too low to justify universal administration, demonstrating how guidelines must constantly balance static trial evidence against dynamic real-world surveillance.

Clinical Landscape

Noteworthy Related Trials

1998

Swedish Pneumococcal Vaccine Trial

n = 3,171 · Lancet

Tested

PPSV23

Population

Adults aged 50 to 85 years previously hospitalized for pneumonia

Comparator

Placebo

Endpoint

Incidence of overall and pneumococcal pneumonia

Key result: The polysaccharide vaccine failed to demonstrate significant efficacy in preventing overall pneumonia or pneumococcal pneumonia in this older population.
2003

Effectiveness of Pneumococcal Polysaccharide Vaccine in Older Adults

n = 47,365 · NEJM

Tested

PPSV23

Population

Immunocompetent adults aged 65 years or older

Comparator

Unvaccinated

Endpoint

Pneumococcal bacteremia

Key result: PPSV23 was highly effective against pneumococcal bacteremia but showed no significant protection against nonbacteremic pneumococcal pneumonia.
2021

PCV20 Phase 3 Trial

n = 3,889 · Clin Infect Dis

Tested

PCV20

Population

Adults aged 60 years and older

Comparator

PCV13 and PPSV23

Endpoint

Opsonophagocytic activity geometric mean titers

Key result: PCV20 demonstrated non-inferior immunogenicity compared to PCV13 for shared serotypes and an acceptable safety profile.

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