New England Journal of Medicine MAY 09, 2019

Progesterone to Prevent Miscarriage in Women with Early Pregnancy Bleeding: The PRISM Trial

Arri Coomarasamy et al.

Bottom Line

In this large, multicenter, double-blind, placebo-controlled trial, vaginal micronised progesterone did not significantly increase the rate of live births among all women presenting with early pregnancy bleeding, although a subgroup analysis suggested benefit for women with a history of recurrent miscarriage.

Key Findings

1. Overall, the primary outcome of live birth at 34 weeks or greater did not differ significantly between groups: 75% in the progesterone group versus 72% in the placebo group (relative rate, 1.03; 95% CI, 1.00 to 1.07; P=0.08).
2. A significant pre-specified subgroup effect was observed based on the number of previous miscarriages (interaction test P=0.007).
3. In participants with a history of three or more prior miscarriages, the live birth rate was 72% in the progesterone group compared to 57% in the placebo group (relative rate, 1.28; 95% CI, 1.08 to 1.51).
4. No significant differences in safety outcomes or adverse events were identified between the treatment and placebo arms.

Study Design

Design
RCT
Double-Blind
Sample
4,153
Patients
Duration
16 wk
Median
Setting
Multicenter, UK
Population Women 16-39 years old with early pregnancy bleeding (<= 12 weeks gestation) and an intrauterine gestational sac.
Intervention Vaginal micronised progesterone (400 mg twice daily) from enrollment until 16 weeks of gestation.
Comparator Matching placebo vaginal suppositories twice daily from enrollment until 16 weeks of gestation.
Outcome Incidence of live birth at 34 weeks of gestation or greater.

Study Limitations

The primary analysis failed to reach statistical significance for the overall study population.
The beneficial effects identified in specific subgroups were based on subgroup analyses, which increase the risk of type I error due to multiple comparisons.
The study was limited to a specific route and dosage (400 mg twice daily, vaginal/rectal) and duration (up to 16 weeks) of progesterone administration.
Post-hoc analyses regarding the history of miscarriage require cautious interpretation and validation in future trials.

Clinical Significance

While progesterone is not indicated for all women presenting with threatened miscarriage, the findings support its use in women with early pregnancy bleeding who have a history of previous miscarriage, leading to updated clinical guidelines (e.g., NICE) in certain jurisdictions.

Historical Context

Before the PRISM trial, smaller studies and meta-analyses provided conflicting data regarding the efficacy of progesterone in treating threatened miscarriage, necessitating a large, robustly designed trial to clarify its role in clinical practice.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

What is the physiological role of progesterone in early pregnancy maintenance, and how does the 'progesterone block' theory justify its use in threatened miscarriage?

Key Response

Progesterone is essential for decidualization of the endometrium and maintaining uterine quiescence by inhibiting myometrial contractions (the 'progesterone block'). The trial investigates whether exogenous progesterone can compensate for potential luteal phase deficiency or stabilize the pregnancy in the face of early bleeding.

Resident
Resident

Based on the PRISM trial results, which specific subgroup of patients presenting with threatened miscarriage should be prioritized for vaginal micronised progesterone, and what is the magnitude of the benefit?

Key Response

While the primary outcome was non-significant for the overall population, the subgroup analysis showed a significant increase in live birth rates for women with a history of recurrent miscarriage (3 or more previous losses), with a live birth rate of 72% in the progesterone group versus 57% in the placebo group (Rate Ratio 1.28).

Fellow
Fellow

Discuss the clinical implications of the 'biological gradient' observed in the PRISM trial regarding the number of previous miscarriages and its impact on the Number Needed to Treat (NNT).

Key Response

The trial demonstrated a clear trend: as the number of previous miscarriages increased, the benefit of progesterone treatment became more pronounced. For women with no previous losses, the NNT was essentially infinite; for those with 1-2 losses, it was roughly 25; and for those with 3 or more losses, the NNT was 7, indicating highly effective targeted therapy.

Attending
Attending

How does the PRISM trial resolve the historical 'harmless but useless' perception of progesterone in early pregnancy, and how should this change our counseling of patients with their first-ever episode of bleeding?

Key Response

PRISM provides high-quality evidence that routine use for all-comers is not indicated, allowing clinicians to avoid unnecessary treatment in low-risk patients. For those with their first bleeding episode and no prior losses, clinicians can confidently counsel that progesterone does not significantly improve outcomes, shifting the focus to expectant management and reassurance.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

Critique the use of a 2% minimum clinically important difference (MCID) in the power calculation of the PRISM trial and discuss how this influence may have led to a 'near-significant' p-value for the primary outcome.

Key Response

The study was powered to detect a 5% difference (75% vs 80%), requiring a large sample size (n=4153). The actual observed difference was 3% (75% vs 72%, p=0.08). A researcher must evaluate if the trial was slightly underpowered for a smaller but potentially still clinically relevant effect, or if the p-value accurately reflects a lack of universal therapeutic efficacy.

Journal Editor
Journal Editor

Given that the primary outcome of the PRISM trial was statistically non-significant (p=0.08), what features of the trial's design and subgroup analysis justify its publication in a high-impact journal like NEJM?

Key Response

The trial's exceptional rigor (multi-center, double-blind, large N), the pre-specification of the miscarriage-history subgroup, and the clear public health importance of the negative primary finding (preventing over-medicalization) make it landmark evidence. Editors value 'definitive negatives' as much as positives in high-frequency clinical scenarios.

Guideline Committee
Guideline Committee

In light of the PRISM trial, how should current NICE or ACOG recommendations be adjusted regarding the use of progesterone in threatened miscarriage, specifically for women with a history of one or more losses?

Key Response

Following PRISM, NICE updated guideline NG126 to recommend 400mg micronized progesterone BID for women with vaginal bleeding and a history of at least one previous miscarriage. This represents a nuanced shift from treating 'everyone' or 'no one' to a 'targeted' evidence-based approach based on obstetric history.

Clinical Landscape

Noteworthy Related Trials

2015

PROMISE Trial

n = 836 · NEJM

Tested

Micronized vaginal progesterone

Population

Women with unexplained recurrent miscarriage

Comparator

Placebo

Endpoint

Live birth rate

Key result: The use of first-trimester vaginal progesterone did not result in a significantly higher rate of live births among women with unexplained recurrent miscarriage.
2018

PICTURE Trial

n = 148 · BJOG

Tested

Vaginal progesterone

Population

Women with early pregnancy bleeding and a history of recurrent miscarriage

Comparator

Placebo

Endpoint

Live birth rate

Key result: Progesterone therapy did not significantly improve live birth rates in this high-risk subgroup.
2019

OPPTIMUM Trial

n = 1228 · Lancet

Tested

Vaginal progesterone

Population

Women at high risk of preterm birth

Comparator

Placebo

Endpoint

Neurodevelopmental outcome at 2 years of age

Key result: Vaginal progesterone did not reduce the risk of preterm birth or improve neurodevelopmental outcomes in high-risk women.

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