The New England Journal of Medicine November 21, 2019

Ticagrelor with or without Aspirin in High-Risk Patients after PCI

Roxana Mehran, Usman Baber, Samin K. Sharma, et al.

Bottom Line

In high-risk patients who underwent PCI and completed 3 months of dual antiplatelet therapy without incident, dropping aspirin and continuing ticagrelor monotherapy significantly reduced clinically relevant bleeding without increasing the risk of death, myocardial infarction, or stroke.

Key Findings

1. Ticagrelor monotherapy reduced the incidence of the primary bleeding endpoint (BARC type 2, 3, or 5) to 4.0% compared to 7.1% with ticagrelor plus aspirin (HR 0.56; 95% CI, 0.45 to 0.68; P<0.001).
2. The incidence of severe bleeding (BARC type 3 or 5) was also significantly lower in the monotherapy group (1.0% vs. 2.0%; HR 0.49; 95% CI, 0.33 to 0.74).
3. The composite ischemic endpoint (death from any cause, nonfatal myocardial infarction, or nonfatal stroke) occurred in 3.9% of patients in both the ticagrelor monotherapy and ticagrelor plus aspirin groups (HR 0.99; 95% CI, 0.78 to 1.25; P<0.001 for noninferiority).

Study Design

Design
Randomized Controlled Trial
Double-Blind
Sample
7,119
Patients
Duration
12 mo
Median
Setting
Multicenter, 11 countries
Population Patients at high risk for bleeding or ischemia who underwent PCI with at least one drug-eluting stent and successfully completed 3 months of ticagrelor plus aspirin without major bleeding or ischemic events.
Intervention Ticagrelor (90 mg twice daily) plus matched placebo for 12 months (from month 3 to month 15 post-PCI).
Comparator Ticagrelor (90 mg twice daily) plus aspirin (81 to 100 mg daily) for 12 months.
Outcome Incidence of Bleeding Academic Research Consortium (BARC) type 2, 3, or 5 bleeding between randomization (3 months post-PCI) and 1 year.

Study Limitations

The randomized population was pre-selected through an initial 3-month open-label run-in period, meaning results only apply to patients who can tolerate early dual antiplatelet therapy without major bleeding or ischemic events.
Patients presenting with ST-segment elevation myocardial infarction (STEMI), cardiogenic shock, or those with a prior stroke were excluded from the trial, limiting generalizability to these ultra-high-risk populations.
While noninferiority was met for the composite ischemic endpoint, the trial was not sufficiently powered to assess small but potentially significant differences in rare individual ischemic events such as stent thrombosis.

Clinical Significance

The TWILIGHT trial established a new standard of care for antithrombotic de-escalation following PCI. By demonstrating that withdrawing aspirin after 3 months of DAPT and continuing ticagrelor monotherapy halves the risk of major bleeding without compromising anti-ischemic efficacy, the trial supports tailored, aspirin-free strategies in high-risk patients to optimize the balance of bleeding and thrombosis.

Historical Context

Historically, standard practice following PCI mandated 6 to 12 months of dual antiplatelet therapy (aspirin plus a P2Y12 inhibitor) to mitigate the risk of stent thrombosis. However, prolonged DAPT drives up bleeding events, which are strongly associated with increased morbidity and mortality. In the era of newer-generation drug-eluting stents (which carry a substantially lower intrinsic risk of thrombosis), the TWILIGHT trial was designed to test whether the bleeding risk of aspirin could be safely eliminated early (at 3 months) by relying on the potent P2Y12 inhibition of ticagrelor alone.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

How does the mechanism of action of ticagrelor differ from that of aspirin, and why might ticagrelor monotherapy provide sufficient platelet inhibition to prevent stent thrombosis without concurrent cyclooxygenase inhibition?

Key Response

Aspirin irreversibly inhibits COX-1, preventing thromboxane A2 generation, while ticagrelor reversibly and directly blocks the P2Y12 ADP receptor. P2Y12 plays a central role in amplifying platelet activation. Potent blockade of P2Y12 by ticagrelor is often sufficient to prevent stent thrombosis, rendering the addition of aspirin redundant for efficacy but additive for bleeding risk, particularly gastrointestinal bleeding due to systemic COX-1 inhibition.

Resident
Resident

When managing a patient after PCI, what clinical or angiographic features defined the 'high-risk' population in the TWILIGHT trial, and how would you practically implement this strategy at a 3-month follow-up visit?

Key Response

TWILIGHT defined high risk via clinical criteria (e.g., age over 65, female sex, troponin-positive ACS, diabetes, CKD) or angiographic criteria (e.g., multivessel CAD, target lesion requiring over 30mm stent, bifurcation, left main). Practically, if a patient matching these criteria presents at 3 months post-PCI with no bleeding or ischemic events, the resident should discontinue aspirin and continue ticagrelor 90 mg twice daily.

Fellow
Fellow

The TWILIGHT trial included patients with NSTEMI and unstable angina but explicitly excluded those presenting with STEMI. As a cardiology fellow, how do you weigh the ischemic risk of dropping aspirin at 3 months in a STEMI patient who underwent complex PCI compared to an NSTEMI patient?

Key Response

STEMI patients generally have a higher early prothrombotic burden and were excluded from TWILIGHT, making direct extrapolation challenging. Fellows must recognize that while TWILIGHT established the safety of dropping aspirin in NSTEMI/stable CAD, applying this to STEMI requires individualized risk assessment, although subsequent trials like TICO have provided more specific evidence supporting P2Y12 monotherapy after 3 months even in STEMI populations.

Attending
Attending

Historically, the standard was to prolong dual antiplatelet therapy in high-ischemic-risk patients, as seen in the DAPT trial. How do you reconcile the TWILIGHT results with the DAPT study, and how does this shift your shared decision-making discussions?

Key Response

The DAPT trial showed extending DAPT reduced ischemia but increased bleeding, primarily using clopidogrel. TWILIGHT utilizes a more potent P2Y12 inhibitor (ticagrelor), which maintains a high ceiling of ischemic protection on its own. This represents a paradigm shift from 'more is better' to 'less is more' regarding aspirin, teaching us that modifying the antiplatelet regimen based on the potency of the P2Y12 inhibitor can successfully mitigate bleeding without sacrificing ischemic safety.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

The TWILIGHT trial utilized a 3-month open-label run-in period before randomization. How does this 'event-free survivor' enrichment strategy impact the internal validity of the study and the statistical power required for the non-inferiority margin of ischemic outcomes?

Key Response

A run-in period depletes the cohort of patients who experience early bleeding or ischemic events, which are most frequent in the first 30 to 90 days. While this maximizes the safety profile of the intervention phase, it lowers the overall event rate. A lower event rate can artificially make non-inferiority easier to achieve if the absolute margin is fixed, and it limits generalizability strictly to patients who have already proven they can tolerate 3 months of DAPT.

Journal Editor
Journal Editor

The TWILIGHT study was primarily powered for superior bleeding outcomes and secondarily for non-inferiority in ischemic events with a non-inferiority margin hazard ratio of 1.6. As an editor, what concerns might you raise regarding this wide margin for the composite ischemic endpoint?

Key Response

A non-inferiority margin of 1.6 means the trial accepted up to a 60 percent relative increase in ischemic events as 'non-inferior.' Although the observed hazard ratio was 0.99, a rigorous peer reviewer would flag that the trial was not sufficiently powered to definitively rule out small but clinically catastrophic increases in stent thrombosis or myocardial infarction, particularly in underrepresented subgroups.

Guideline Committee
Guideline Committee

Based on the TWILIGHT trial and similar contemporary data, how should ACC/AHA and ESC guidelines be updated regarding the duration of aspirin therapy post-PCI in high-risk patients, and what Class of Recommendation should be assigned?

Key Response

The TWILIGHT trial directly influenced the 2021 ACC/AHA and 2020 ESC guidelines. Based on this evidence, dropping aspirin after 1 to 3 months of DAPT and continuing a P2Y12 inhibitor (like ticagrelor) in patients who are event-free and not at high bleeding risk is now given a Class IIa recommendation (Level of Evidence A). This updates older guidelines that rigidly recommended 12 months of DAPT for all ACS patients, shifting toward individualized bleeding reduction strategies.

Clinical Landscape

Noteworthy Related Trials

2018

GLOBAL LEADERS

n = 15,968 · Lancet

Tested

1 month DAPT followed by 23 months ticagrelor monotherapy

Population

Patients undergoing PCI with a biolimus A9-eluting stent

Comparator

12 months standard DAPT followed by 12 months aspirin

Endpoint

All-cause mortality or non-fatal new Q-wave MI at 2 years

Key result: Ticagrelor monotherapy following 1 month of DAPT did not show superiority over standard DAPT in reducing the primary ischemic endpoint.
2019

STOPDAPT-2

n = 3,045 · JAMA

Tested

1 month DAPT followed by clopidogrel monotherapy

Population

Patients undergoing PCI

Comparator

12 months standard DAPT

Endpoint

Composite of cardiovascular death, MI, ischemic stroke, stent thrombosis, or TIMI major/minor bleeding at 12 months

Key result: One month of DAPT followed by clopidogrel monotherapy was superior to 12 months of DAPT for the net composite ischemic and bleeding endpoint.
2020

TICO

n = 3,056 · JAMA

Tested

3 months DAPT followed by ticagrelor monotherapy

Population

Patients with acute coronary syndromes undergoing PCI

Comparator

12 months ticagrelor-based DAPT

Endpoint

Net adverse clinical events (TIMI major bleeding and MACE) at 12 months

Key result: Ticagrelor monotherapy after 3 months of DAPT significantly reduced net adverse clinical events, mainly driven by reduced major bleeding without increasing ischemic risk.

Tailored to your role

Want this tailored to you?

Add your specialty or training stage to get role-specific takeaways and more questions.

Personalize this analysis