The New England Journal of Medicine June 26, 2024

Amivantamab plus Lazertinib in Previously Untreated EGFR-Mutated Advanced NSCLC

Byoung Chul Cho et al.

Bottom Line

The phase 3 MARIPOSA trial demonstrated that first-line treatment with amivantamab plus lazertinib significantly prolonged progression-free survival compared to osimertinib in patients with EGFR-mutated advanced non-small-cell lung cancer, though with increased toxicity.

Key Findings

1. The median progression-free survival was significantly longer in the amivantamab-lazertinib group than in the osimertinib group (23.7 vs. 16.6 months; hazard ratio, 0.70; 95% CI, 0.58 to 0.85; P<0.001) [1.1.4].
2. Objective response rates were comparable between the amivantamab-lazertinib group (86%) and the osimertinib group (85%).
3. Among patients with a confirmed response, the median duration of response was notably longer with amivantamab-lazertinib (25.8 months) than with osimertinib (16.8 months).
4. In a planned interim analysis of overall survival, the hazard ratio for death for amivantamab-lazertinib compared with osimertinib was 0.80 (95% CI, 0.61 to 1.05), which did not cross the prespecified threshold for statistical significance.
5. The incidence of discontinuation of all agents due to treatment-related adverse events was higher with the combination regimen (10% with amivantamab-lazertinib) compared to standard monotherapy (3% with osimertinib).

Study Design

Design
Phase 3 RCT
Open-Label (Primary Comparison)
Sample
1,074
Patients
Duration
22.0 mo
Median
Setting
International, multicenter
Population Patients aged 18 or older with previously untreated, locally advanced or metastatic non-small-cell lung cancer (NSCLC) harboring EGFR exon 19 deletion or L858R substitution mutations.
Intervention Amivantamab (intravenous EGFR-MET bispecific antibody) plus lazertinib (oral third-generation EGFR TKI)
Comparator Osimertinib monotherapy (a third blinded arm also evaluated lazertinib monotherapy)
Outcome Progression-free survival (PFS) as assessed by blinded independent central review

Study Limitations

The primary experimental arm (amivantamab plus lazertinib) was open-label, which could potentially introduce bias, although the primary endpoint of progression-free survival was assessed by blinded independent central review.
The combination regimen is associated with notably higher rates of grade 3 or higher adverse events (e.g., venous thromboembolism, severe rash, and infusion-related reactions) than osimertinib, requiring intensive prophylactic measures such as anticoagulation and dermatologic management.
Intravenous administration of amivantamab introduces an increased logistical burden and requires longer clinic visits compared to the all-oral osimertinib regimen.
At the time of the primary publication, overall survival data were immature, meaning the ultimate mortality benefit of the upfront combination over sequential therapy remains to be definitively proven.

Clinical Significance

The MARIPOSA trial establishes amivantamab plus lazertinib as a highly effective, chemotherapy-free frontline combination for patients with EGFR-mutated advanced NSCLC. By dual-targeting the EGFR and MET pathways, the regimen achieves a clinically meaningful delay in disease progression and prolonged response duration compared to osimertinib. However, clinicians must carefully weigh this superior progression-free survival against the meaningfully increased toxicity profile and logistical requirements when counseling treatment-naive patients.

Historical Context

Following the landmark FLAURA trial in 2018, the third-generation EGFR tyrosine kinase inhibitor (TKI) osimertinib became the undisputed standard of care for first-line treatment of advanced NSCLC with classical EGFR mutations (exon 19 deletion or L858R). Despite deep initial responses, virtually all patients eventually develop resistance, frequently driven by secondary EGFR pathway alterations or MET amplification. Amivantamab, an EGFR-MET bispecific antibody, combined with lazertinib, a CNS-penetrant third-generation EGFR TKI, was hypothesized to preemptively block these dominant escape pathways. The MARIPOSA trial represents a broader modern paradigm shift in thoracic oncology—similar to the FLAURA2 trial evaluating upfront osimertinib plus chemotherapy—testing whether upfront combinatorial strategies can yield deeper, more durable tumor suppression than sequential monotherapy.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

How does the dual mechanism of amivantamab and lazertinib target EGFR-mutated NSCLC differently than osimertinib monotherapy, and why is the addition of MET inhibition important pathophysiologically?

Key Response

Amivantamab is a bispecific antibody targeting both EGFR extracellular domains and the MET receptor, while lazertinib is a 3rd-generation EGFR tyrosine kinase inhibitor (TKI). Combining them targets the EGFR pathway from both the inside (kinase domain) and outside (extracellular domain), promoting receptor degradation. Additionally, MET amplification is a primary bypass-track resistance mechanism to osimertinib; by inhibiting MET upfront, amivantamab preemptively blocks this common escape route.

Resident
Resident

Given the increased toxicity profile of the amivantamab plus lazertinib combination demonstrated in the MARIPOSA trial, how should this affect your patient selection and required prophylactic management in the first-line setting compared to starting osimertinib?

Key Response

The MARIPOSA trial showed significantly higher rates of venous thromboembolism (VTE), rash, and infusion-related reactions with the combination. Residents must recognize that initiating this regimen requires mandatory prophylactic anticoagulation for the first four months and intense monitoring for infusion reactions (especially on Cycle 1 Day 1). Patient comorbidities, such as bleeding risk, frailty, and ability to attend frequent IV infusion visits, must heavily influence the shared decision-making process when choosing between this combination and standard-of-care daily oral osimertinib.

Fellow
Fellow

Osimertinib is highly valued for its central nervous system (CNS) penetration. How does the amivantamab plus lazertinib combination compare in terms of intracranial efficacy, and how might this combination alter the expected clonal evolution and subsequent resistance mechanisms upon progression?

Key Response

Lazertinib is a highly CNS-penetrant TKI comparable to osimertinib, ensuring intracranial disease control, which is critical in EGFR+ NSCLC. By preemptively targeting MET and inducing EGFR down-regulation with amivantamab, the combination likely shifts the evolutionary pressure of the tumor, steering the resistance landscape away from classical MET amplification and secondary EGFR mutations (like C797S). This may lead to an increase in uncharacterized off-target resistance mechanisms, histologic transformations (e.g., small cell transformation), or acquired resistance requiring entirely novel salvage strategies.

Attending
Attending

With progression-free survival (PFS) significantly prolonged but overall survival (OS) data still immature, how do we justify shifting the first-line paradigm from a highly tolerable single-agent (osimertinib) to a more toxic combination regimen, especially considering the implications for subsequent treatment sequencing?

Key Response

This addresses the classic oncology dilemma: upfront PFS benefit versus quality of life (QoL) and long-term OS. If the combination is used upfront, patients face early toxicity and mandatory prophylactic anticoagulation. If mature OS ultimately does not prove superior to sequential therapy (e.g., osimertinib upfront followed by amivantamab plus chemotherapy upon progression, as explored in MARIPOSA-2), the upfront toxicity may not be justified. Attendings must weigh whether to use the 'best drugs first' to maximize the initial progression-free interval or preserve QoL by reserving combination regimens for the second-line setting.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

The MARIPOSA trial utilized a lazertinib monotherapy arm to isolate the contribution of amivantamab. From a statistical and trial design perspective, how does this 3-arm design strengthen causal inference for the combination regimen's efficacy, and what are the limitations in statistical power regarding the monotherapy comparison?

Key Response

Regulatory agencies increasingly require 'contribution of components' analyses for combination regimens. Including a lazertinib arm ensures the superiority of amivantamab+lazertinib over osimertinib isn't simply because lazertinib is a vastly superior TKI (though early data showed them to be similarly effective). However, the trial was primarily powered for the combination versus osimertinib comparison; the lazertinib versus osimertinib data is largely descriptive. This limits definitive statistical conclusions about the two TKIs head-to-head, highlighting the trade-offs in sample size allocation and alpha spending in complex multi-arm phase 3 trials.

Journal Editor
Journal Editor

Because amivantamab requires intravenous administration and intensive monitoring, blinding between the combination arm and the oral osimertinib arm is practically challenging. How might the disparity in healthcare interaction frequency introduce bias into the reporting of subjective adverse events and investigator-assessed progression, and what methodological safeguards should reviewers demand?

Key Response

The combination arm requires frequent IV visits, whereas osimertinib is a daily pill. This disparity can lead to detection bias (e.g., finding asymptomatic progressions earlier due to more frequent scans or clinical encounters) and reporting bias for subjective adverse events. A rigorous reviewer must scrutinize the concordance between investigator-assessed PFS and Blinded Independent Central Review (BICR) to ensure the primary endpoint is robust against this bias, and evaluate whether the protocol matched the frequency of imaging assessments perfectly across both arms.

Guideline Committee
Guideline Committee

Should amivantamab plus lazertinib be designated as a 'Category 1, Preferred' regimen alongside osimertinib in the NCCN/ASCO guidelines for first-line EGFR-mutated advanced NSCLC, or does the toxicity profile mandate a different tier of recommendation pending overall survival data?

Key Response

Currently, osimertinib is the universally preferred Category 1 first-line option based on the FLAURA trial, due to its excellent efficacy and tolerability. While MARIPOSA shows amivantamab+lazertinib has superior PFS, the higher toxicity (VTE, infusion reactions) and lack of mature OS data complicate its standing. Guideline committees must deliberate whether this combination shares the 'Preferred' status, or if it should be listed as 'Other Recommended' or reserved for specific subgroups. The recommendation text must heavily emphasize shared decision-making, weighing a median 7-month PFS advantage against the burden of IV therapy, rash, and prophylactic anticoagulation.

Clinical Landscape

Noteworthy Related Trials

2018

FLAURA Trial

n = 556 · NEJM

Tested

Osimertinib 80mg daily

Population

Previously untreated EGFR-mutated advanced NSCLC

Comparator

Gefitinib or Erlotinib

Endpoint

Progression-free survival (PFS)

Key result: Osimertinib significantly improved median PFS compared to standard EGFR TKIs (18.9 vs 10.2 months).
2023

FLAURA2 Trial

n = 557 · NEJM

Tested

Osimertinib plus platinum-based chemotherapy

Population

Previously untreated EGFR-mutated advanced NSCLC

Comparator

Osimertinib monotherapy

Endpoint

Progression-free survival (PFS)

Key result: The addition of chemotherapy to osimertinib significantly prolonged PFS (25.5 vs 16.7 months) but resulted in higher toxicity.
2023

LASER301 Trial

n = 393 · JCO

Tested

Lazertinib 240mg daily

Population

Previously untreated EGFR-mutated advanced NSCLC

Comparator

Gefitinib 250mg daily

Endpoint

Progression-free survival (PFS)

Key result: Lazertinib demonstrated superior PFS compared to gefitinib (20.6 vs 9.7 months) with a manageable safety profile.

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