New England Journal of Medicine NOVEMBER 21, 2019

Dapagliflozin in Patients with Heart Failure and Reduced Ejection Fraction

McMurray JJV, Solomon SD, Inzucchi SE, et al.

Bottom Line

In patients with heart failure and reduced ejection fraction, the addition of dapagliflozin to standard therapy significantly reduced the risk of worsening heart failure and cardiovascular death, regardless of the patient's diabetes status.

Key Findings

1. Theprimarycompositeoutcome(worseningheartfailureorcardiovasculardeath)occurredin16.3%ofthedapagliflozingroupcomparedto21.2%oftheplacebogroup(HR0.74;95%CI0.65-0.85;P<0.001)[1.4].
2. A first worsening heart failure event was significantly reduced in the dapagliflozin group (10.0%) versus placebo (13.7%) (HR 0.70; 95% CI 0.59-0.83).
3. Death from cardiovascular causes occurred in 9.6% of patients in the dapagliflozin arm compared to 11.5% in the placebo arm (HR 0.82; 95% CI 0.69-0.98).
4. All-cause mortality was significantly lower in the dapagliflozin group (11.6%) than in the placebo group (13.9%) (HR 0.83; 95% CI 0.71-0.97).
5. The cardioprotective benefits were remarkably consistent across all prespecified subgroups, proving equally efficacious in patients with and without type 2 diabetes.

Study Design

Design
RCT
Double-Blind
Sample
4,744
Patients
Duration
18.2 mo
Median
Setting
20 countries
Population Adults with symptomatic (NYHA class II-IV) heart failure and an ejection fraction ≤40% (HFrEF), with elevated NT-proBNP levels, who were receiving stable, recommended heart failure therapy.
Intervention Dapagliflozin 10 mg once daily
Comparator Matching placebo once daily
Outcome Composite of worsening heart failure (hospitalization or an urgent visit resulting in intravenous therapy for heart failure) or cardiovascular death.

Study Limitations

Limited racial diversity within the study cohort (approximately 70% of participants were White, while only 5% were Black), potentially limiting the generalizability of the findings to more diverse populations [1.2].
Exclusion of patients with severe renal impairment (eGFR <30 ml/min/1.73 m2) limited conclusions regarding efficacy and safety in patients with advanced chronic kidney disease.
Patients with symptomatic hypotension or a systolic blood pressure <95 mmHg were excluded, preselecting for a hemodynamically stable HFrEF population.

Clinical Significance

DAPA-HF fundamentally shifted the paradigm of heart failure management by establishing SGLT2 inhibitors as a core, foundational pillar of guideline-directed medical therapy (GDMT) for heart failure with reduced ejection fraction (HFrEF). It demonstrated definitively that the prognostic benefits of dapagliflozin are driven by direct cardioprotective mechanisms rather than glucose-lowering effects, thus broadening its indication beyond endocrinology into mainstream cardiology.

Historical Context

SGLT2 inhibitors were initially developed as oral hypoglycemic agents for type 2 diabetes. Cardiovascular outcome trials mandated by the FDA (such as EMPA-REG OUTCOME, CANVAS, and DECLARE-TIMI 58) revealed unexpected and dramatic reductions in heart failure hospitalizations among diabetic patients. DAPA-HF was the first landmark trial to formally investigate whether these profound benefits would extend to patients with established HFrEF who did not have diabetes. The trial confirmed this hypothesis, sparking a revolution where a traditional 'diabetes drug' became a primary treatment for heart failure.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

Dapagliflozin is an SGLT2 inhibitor originally developed for glycemic control in diabetes. Based on the DAPA-HF trial showing profound cardiovascular benefits regardless of diabetes status, what are the primary proposed mechanisms by which SGLT2 inhibitors improve outcomes in heart failure with reduced ejection fraction (HFrEF)?

Key Response

While SGLT2 inhibitors block glucose reabsorption in the proximal tubule leading to glycosuria, their HF benefits are independent of HbA1c reduction. Proposed mechanisms include osmotic diuresis and natriuresis (which reduce cardiac preload without causing severe intravascular volume depletion), a shift in myocardial energetics toward more efficient ketone utilization, reduction in sympathetic nervous system activity, and decreased interstitial myocardial fibrosis.

Resident
Resident

When initiating dapagliflozin in a patient with HFrEF who is already receiving high-dose loop diuretics, what clinical parameters must you closely monitor, and how does the patient's diabetes status alter your counseling regarding adverse effects?

Key Response

Residents must monitor volume status and renal function, as dapagliflozin causes mild osmotic diuresis and a characteristic initial (but reversible) 'dip' in eGFR. Diuretic doses may need to be downtitrated to prevent hypotension or AKI. For counseling, diabetic patients must be warned about genital mycotic infections and euglycemic diabetic ketoacidosis (DKA); however, non-diabetic patients should be reassured that their risk for DKA and clinically significant hypoglycemia is negligible.

Fellow
Fellow

In the DAPA-HF trial, a subset of the patient population was receiving sacubitril/valsartan (an ARNI) at baseline. How does the addition of dapagliflozin to an ARNI impact clinical outcomes, and what does this imply about the pathophysiological pathways targeted by foundational HFrEF therapies?

Key Response

Subgroup analyses of DAPA-HF demonstrated that the hazard ratio for the primary outcome was consistent whether or not patients were taking an ARNI at baseline. This implies that SGLT2 inhibitors operate through distinct, synergistic pathophysiologic pathways (e.g., modified sodium-hydrogen exchange, altered myocardial metabolism) rather than duplicating the neurohormonal blockade of RAAS and neprilysin inhibition, thereby justifying the simultaneous use of all 'four pillars' of guideline-directed medical therapy (GDMT).

Attending
Attending

DAPA-HF fundamentally changed the categorization of SGLT2 inhibitors from purely endocrine therapies to primary cardiovascular therapies. How should this conceptual shift overcome 'therapeutic inertia' in your practice, and what are the practical barriers to rapid, simultaneous initiation of GDMT?

Key Response

Attendings should use this trial to move away from the historical 'stepwise' delayed addition of HF drugs and advocate for rapid, simultaneous initiation of the four foundational pillars. Barriers include the residual perception of SGLT2 inhibitors as 'diabetes drugs' causing prescribing hesitation among cardiologists, polypharmacy concerns, and cost or prior authorization hurdles. Framing dapagliflozin as a life-saving cardiovascular drug is essential to overcoming this inertia.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

DAPA-HF utilized a composite primary endpoint evaluated via a traditional time-to-first-event Cox proportional-hazards model. From a biostatistical perspective, what are the limitations of this approach in chronic heart failure trials, and how might recurrent event analyses or hierarchical win ratios alter the interpretation of the drug's true efficacy?

Key Response

A time-to-first-event analysis treats a heart failure hospitalization and cardiovascular death equally and ignores all subsequent hospitalizations, which heavily underrepresents the total longitudinal disease burden. Utilizing recurrent event models (e.g., Lin-Wei-Yang-Ying) or a hierarchical win ratio (which prioritizes mortality over morbidity) would provide a more comprehensive, statistically robust reflection of the intervention's capacity to reduce total healthcare utilization and cumulative patient suffering.

Journal Editor
Journal Editor

As a critical peer reviewer evaluating the DAPA-HF manuscript, what concerns might you raise regarding the baseline background medical therapy of the trial cohort, and how could this impact the external validity and effect size of the intervention in a contemporary heart failure population?

Key Response

A seasoned reviewer would flag that while beta-blocker and ACEi/ARB use was excellent, the baseline use of sacubitril/valsartan (ARNI) was quite low (approximately 11%). The editor would question whether the striking relative risk reduction observed with dapagliflozin is artificially inflated by comparing it to a control group that is arguably 'under-treated' by optimal modern standards, demanding robust prespecified subgroup analyses to confirm additive benefit.

Guideline Committee
Guideline Committee

Following the publication of DAPA-HF and corroborated by EMPEROR-Reduced, how did the 2022 AHA/ACC/HFSA Heart Failure Guidelines update their recommendations regarding SGLT2 inhibitors, and what specific Class of Recommendation (COR) and Level of Evidence (LOE) were established?

Key Response

The profound, consistent benefits seen in DAPA-HF independent of diabetes status mandated a major guideline update. In the 2022 AHA/ACC/HFSA guidelines, SGLT2 inhibitors (dapagliflozin or empagliflozin) were elevated to a Class 1, Level of Evidence A recommendation. The guidelines explicitly state they should be used in patients with symptomatic chronic HFrEF to reduce hospitalization for heart failure and cardiovascular mortality, officially cementing them as an indispensable pillar of GDMT.

Clinical Landscape

Noteworthy Related Trials

2014

PARADIGM-HF

n = 8,399 · NEJM

Tested

Sacubitril/valsartan 200mg twice daily

Population

Patients with heart failure and reduced ejection fraction (HFrEF)

Comparator

Enalapril 10mg twice daily

Endpoint

Composite of cardiovascular death or hospitalization for heart failure

Key result: Sacubitril/valsartan was superior to enalapril in reducing the risks of death and of hospitalization for heart failure.
2020

EMPEROR-Reduced

n = 3,730 · NEJM

Tested

Empagliflozin 10mg daily

Population

Patients with heart failure and reduced ejection fraction (HFrEF) with or without T2DM

Comparator

Placebo

Endpoint

Composite of cardiovascular death or hospitalization for worsening heart failure

Key result: Empagliflozin significantly reduced the risk of cardiovascular death or hospitalization for heart failure compared to placebo.
2022

DELIVER

n = 6,263 · NEJM

Tested

Dapagliflozin 10mg daily

Population

Patients with heart failure and mildly reduced or preserved ejection fraction (HFmrEF/HFpEF)

Comparator

Placebo

Endpoint

Composite of cardiovascular death or worsening heart failure

Key result: Dapagliflozin significantly reduced the composite risk of cardiovascular death or worsening heart failure in patients with mildly reduced or preserved ejection fraction.

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