The Lancet August 26, 2023

Oral semaglutide 50 mg taken once per day in adults with overweight or obesity (OASIS 1): a randomised, double-blind, placebo-controlled, phase 3 trial

Knop FK, Aroda VR, do Vale RD, et al.

Bottom Line

In adults with overweight or obesity without type 2 diabetes, once-daily oral semaglutide 50 mg combined with a lifestyle intervention resulted in a clinically meaningful 15.1% reduction in body weight at 68 weeks, demonstrating efficacy comparable to subcutaneous formulations.

Key Findings

1. At week 68, the estimated mean body weight change from baseline was -15.1% with oral semaglutide 50 mg versus -2.4% with placebo (estimated treatment difference of -12.7 percentage points; p<0.0001) [1.1.5].
2. A significantly higher proportion of participants in the oral semaglutide group achieved a body weight reduction of ≥5% compared to the placebo group (85% vs 26%; p<0.0001).
3. Adverse events were reported in 92% of participants receiving oral semaglutide compared to 86% receiving placebo.
4. The safety profile was consistent with other GLP-1 receptor agonists, with mild-to-moderate gastrointestinal events (e.g., nausea) being the most frequently reported adverse events.

Study Design

Design
RCT
Double-Blind
Sample
667
Patients
Duration
68 wk
Median
Setting
9 countries
Population Adults with a body mass index (BMI) of ≥30 kg/m², or ≥27 kg/m² with at least one weight-related complication or comorbidity, without type 2 diabetes.
Intervention Oral semaglutide escalated to 50 mg once daily, plus a lifestyle intervention.
Comparator Visually matching placebo once daily, plus a lifestyle intervention.
Outcome Co-primary endpoints were the percentage change in body weight from baseline to week 68, and the achievement of a body weight reduction of ≥5% at week 68.

Study Limitations

The 68-week trial duration is insufficient to determine the long-term durability of weight loss or the impact on major adverse cardiovascular events (MACE).
The study population lacked broad diversity, being predominantly female (74%) and predominantly white, which may limit the generalizability of the findings across broader demographic groups.
Gastrointestinal adverse events were highly prevalent and may lead to higher rates of discontinuation or non-adherence in a real-world clinical setting compared to a highly controlled trial environment.
Oral semaglutide requires strict administration protocols (taken on an empty stomach with a small amount of water, followed by a waiting period before eating or taking other medications), which may present a substantial adherence barrier compared to once-weekly injections.

Clinical Significance

OASIS 1 is a landmark trial demonstrating that an oral formulation of a GLP-1 receptor agonist can achieve a magnitude of weight loss (~15%) previously only seen with injectable therapies like subcutaneous semaglutide 2.4 mg (Wegovy). By offering a highly effective non-injectable alternative, high-dose oral semaglutide stands to significantly expand access and adherence for patients with obesity who have needle phobia or a strong preference for oral medications.

Historical Context

The treatment of obesity was revolutionized by the STEP clinical trial program, which established once-weekly subcutaneous semaglutide 2.4 mg as a potent weight-loss therapy. However, the injectable route remained a psychological and logistical barrier for many patients. While oral semaglutide was already approved at lower doses (up to 14 mg daily, marketed as Rybelsus) for type 2 diabetes management, its weight-loss effects at those doses were modest. The OASIS 1 trial was pivotal in bridging this gap, testing a specifically escalated 50 mg high-dose oral formulation to parallel the profound metabolic and weight-loss effects of the injectable forms.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

How does the formulation of oral semaglutide overcome the typical degradation of peptide-based drugs in the gastrointestinal tract, and what is its primary central mechanism of action for weight loss?

Key Response

Oral semaglutide is co-formulated with SNAC (sodium N-(8-[2-hydroxybenzoyl] amino) caprylate), an absorption enhancer that locally increases gastric pH to prevent proteolytic degradation and facilitates transcellular absorption across the gastric mucosa. Centrally, as a GLP-1 receptor agonist, it targets areas like the hypothalamus to increase satiety, delay gastric emptying, and decrease hunger, leading to a significant reduction in caloric intake.

Resident
Resident

The OASIS 1 trial utilizes a 50 mg daily dose of oral semaglutide, which is significantly higher than the 14 mg maximum dose currently approved for type 2 diabetes. How should this difference influence your patient counseling regarding dose titration and the management of gastrointestinal adverse effects?

Key Response

The high 50 mg dose required to achieve a 15.1% weight loss necessitates a prolonged and careful titration schedule (e.g., escalating through 3, 7, 14, and 25 mg) to mitigate severe gastrointestinal adverse events like nausea and vomiting. Residents must counsel patients on strict adherence to the dosing requirements (taking it on an empty stomach with a small amount of water and waiting 30 minutes before eating or taking other medications) to ensure absorption, while modifying diet to manage nausea.

Fellow
Fellow

Given that the 15.1% weight loss seen with 50 mg oral semaglutide in OASIS 1 closely mirrors the results of the STEP 1 trial for subcutaneous semaglutide 2.4 mg, how would you phenotype or select patients for the oral versus subcutaneous route factoring in pharmacokinetics, compliance barriers, and comorbidities?

Key Response

Selection requires shared decision-making based on patient lifestyle and preferences. The oral route democratizes access for patients with needle phobia but demands strict daily fasting compliance (empty stomach, 30-minute wait), which can be a barrier for patients with polypharmacy, erratic morning schedules, or cognitive impairment. Conversely, the once-weekly subcutaneous injection circumvents GI absorption variables and daily routine barriers, potentially offering better long-term adherence for certain demographics.

Attending
Attending

While the OASIS 1 trial demonstrates excellent efficacy, the introduction of a high-dose oral GLP-1 RA brings significant cost, manufacturing, and primary-care integration implications. How does this formulation shift our paradigm of obesity management from a subspecialty intervention to a generalized chronic disease model?

Key Response

An effective oral formulation removes the logistical barrier of injectable therapy training, empowering primary care physicians to prescribe it as easily as anti-hypertensives or statins, further cementing obesity as a primary chronic disease. However, the 50 mg dose requires a massive amount of active pharmaceutical ingredient (API) compared to the 2.4 mg injection, which attendings must recognize will strain global peptide manufacturing and potentially exacerbate drug shortages and healthcare system costs.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

The OASIS 1 trial reports both a 'trial product estimand' (assuming all patients adhered to treatment) and a 'treatment policy estimand' (intention-to-treat, regardless of adherence). How does the differential discontinuation rate due to adverse events between the semaglutide and placebo groups impact the interpretation of these estimands, and what statistical imputation methods are most appropriate?

Key Response

High GI-related discontinuation in the 50 mg group can artificially inflate the perceived efficacy if only the trial product estimand is emphasized. The treatment policy estimand provides a more pragmatic, real-world measure of effectiveness but relies on complex statistical handling of missing data. Pattern-mixture models or multiple imputation must be scrutinized to ensure they appropriately account for data missing not at random (MNAR), as patients dropping out due to side effects likely have different weight trajectories than those completing the trial.

Journal Editor
Journal Editor

Given the prominent gastrointestinal side effect profile of 50 mg oral semaglutide, how might functional unblinding compromise the internal validity of the OASIS 1 trial, and what specific analyses should peer reviewers demand to assess the true impact of the concurrent lifestyle intervention?

Key Response

Because a large percentage of participants on high-dose GLP-1 RAs experience noticeable side effects like nausea or early satiety, true blinding is nearly impossible (functional unblinding). This realization can alter participant behavior, causing those who know they are on the active drug to adhere more strictly to the lifestyle intervention, confounding the drug's direct metabolic effect. Reviewers should look for sensitivity analyses adjusting for GI adverse events or objective markers of lifestyle adherence to isolate the pharmacological efficacy.

Guideline Committee
Guideline Committee

Current major obesity guidelines (such as those from AACE and AHA/ACC/TOS) strongly recommend GLP-1 RAs for chronic weight management based primarily on data from subcutaneous formulations. Based on the OASIS 1 data, how should future guidelines position oral semaglutide 50 mg in the treatment algorithm?

Key Response

OASIS 1 provides high-quality Phase 3 RCT evidence (Level 1a) that oral semaglutide 50 mg yields clinically meaningful weight loss (15.1%) comparable to existing first-line injectable therapies. Guidelines should be updated to include high-dose oral semaglutide as a Class I, Level A recommendation alongside subcutaneous semaglutide 2.4 mg and tirzepatide. The guidelines should explicitly emphasize the importance of shared decision-making regarding the route of administration, highlighting the strict daily dosing conditions required for the oral formulation.

Clinical Landscape

Noteworthy Related Trials

2021

STEP 1

n = 1,961 · NEJM

Tested

Subcutaneous semaglutide 2.4 mg weekly

Population

Adults with overweight or obesity without diabetes

Comparator

Placebo

Endpoint

Percentage change in body weight and proportion achieving >=5% weight reduction

Key result: Participants receiving semaglutide 2.4 mg achieved a mean weight loss of 14.9% compared to 2.4% with placebo at 68 weeks.
2022

SURMOUNT-1

n = 2,539 · NEJM

Tested

Subcutaneous tirzepatide (5 mg, 10 mg, or 15 mg weekly)

Population

Adults with overweight or obesity without diabetes

Comparator

Placebo

Endpoint

Percentage change in body weight and proportion achieving >=5% weight reduction

Key result: Tirzepatide led to a substantial and sustained reduction in body weight, with the 15 mg dose achieving up to 20.9% mean weight loss at 72 weeks.
2023

SELECT

n = 17,604 · NEJM

Tested

Subcutaneous semaglutide 2.4 mg weekly

Population

Adults with overweight or obesity and preexisting cardiovascular disease, without diabetes

Comparator

Placebo

Endpoint

Major adverse cardiovascular events (MACE)

Key result: Semaglutide 2.4 mg reduced the risk of major adverse cardiovascular events by 20% compared to placebo over a mean follow-up of 39.8 months.

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