New England Journal of Medicine July 16, 2015

Effect of Sitagliptin on Cardiovascular Outcomes in Type 2 Diabetes

Jennifer B. Green, Angelyn M. Bethel, Paul W. Armstrong, et al.

Bottom Line

In patients with type 2 diabetes and established cardiovascular disease, adding the DPP-4 inhibitor sitagliptin to usual care did not increase the risk of major adverse cardiovascular events or hospitalization for heart failure.

Key Findings

1. The primary composite cardiovascular outcome (cardiovascular death, nonfatal myocardial infarction, nonfatal stroke, or hospitalization for unstable angina) occurred in 11.4% (4.06 per 100 person-years) of the sitagliptin group and 11.6% (4.17 per 100 person-years) of the placebo group [1.1.4].
2. Sitagliptin was noninferior to placebo for the primary outcome (Hazard Ratio [HR] 0.98; 95% CI, 0.88 to 1.09; P<0.001 for noninferiority).
3. Rates of hospitalization for heart failure were identical between the two groups at 3.1% (HR 1.00; 95% CI, 0.83 to 1.20; P=0.98).
4. Sitagliptin resulted in a small reduction in glycated hemoglobin levels (least-squares mean difference vs. placebo of -0.29 percentage points).
5. There were no significant between-group differences in the incidence rates of acute pancreatitis (P=0.07) or pancreatic cancer (P=0.32).

Study Design

Design
RCT
Double-Blind
Sample
14,671
Patients
Duration
3.0 yr
Median
Setting
38 countries
Population Patients with type 2 diabetes and established cardiovascular disease (HbA1c 6.5-8.0%)
Intervention Sitagliptin added to usual antihyperglycemic care
Comparator Placebo added to usual antihyperglycemic care
Outcome Composite of cardiovascular death, nonfatal myocardial infarction, nonfatal stroke, or hospitalization for unstable angina

Study Limitations

The median follow-up of 3.0 years was relatively short, limiting the ability to assess long-term safety profiles, particularly for delayed adverse events like cancer.
The trial utilized a glycemic equipoise design (allowing adjustments to background therapies), which minimized HbA1c differences between arms to strictly test drug safety, precluding an evaluation of cardiovascular benefits derived from intensive glucose lowering.
The study excluded patients with severe renal insufficiency (estimated glomerular filtration rate <30 mL/min/1.73 m2), limiting the generalizability of the findings in this high-risk subset.

Clinical Significance

TECOS provided critical clinical reassurance regarding the cardiovascular safety of sitagliptin. Most notably, it alleviated concerns regarding a potential class-wide risk of heart failure hospitalization that had been raised by earlier trials of other DPP-4 inhibitors (specifically saxagliptin in SAVOR-TIMI 53). The neutral effect on MACE and heart failure cemented sitagliptin as a safe add-on option for glycemic control in diabetic patients with high baseline cardiovascular risk.

Historical Context

Following the cardiovascular safety controversy surrounding rosiglitazone, the FDA issued a landmark 2008 guidance requiring all new type 2 diabetes therapies to demonstrate cardiovascular safety through dedicated outcomes trials (CVOTs). Early DPP-4 inhibitor CVOTs, such as SAVOR-TIMI 53 (2013), unexpectedly showed a 27% increased risk of hospitalization for heart failure with saxagliptin. TECOS was heavily anticipated as a means to determine whether this heart failure signal was a class effect. By proving that sitagliptin did not carry this risk, TECOS preserved the clinical utility of the DPP-4 inhibitor class.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

What is the mechanism of action of sitagliptin, and physiologically, why was cardiovascular safety a specific concern that prompted large outcome trials like TECOS in the first place?

Key Response

Sitagliptin inhibits dipeptidyl peptidase-4 (DPP-4), an enzyme that degrades incretin hormones like GLP-1 and GIP, thereby enhancing glucose-dependent insulin secretion. The FDA mandated cardiovascular outcome trials (CVOTs) for all new diabetes drugs after rosiglitazone raised concerns about ischemic risk. Furthermore, DPP-4 is widely expressed on vascular endothelium and cardiomyocytes (as CD26), raising mechanistic questions about potential direct cardiovascular effects independent of glycemic control.

Resident
Resident

How do the heart failure findings in the TECOS trial for sitagliptin compare to the SAVOR-TIMI 53 trial for saxagliptin, and how does this influence your management of a diabetic patient with established heart failure?

Key Response

SAVOR-TIMI 53 showed an unexpected increased risk of hospitalization for heart failure with saxagliptin. TECOS was practice-affirming because it demonstrated sitagliptin did not increase heart failure risk, indicating this was not a class effect. Clinically, if a DPP-4 inhibitor is needed, sitagliptin is safer for heart failure patients; however, SGLT2 inhibitors are the guideline-directed first choice in this population due to proven mortality and heart failure benefits.

Fellow
Fellow

Given that both DPP-4 inhibitors and GLP-1 receptor agonists enhance the incretin pathway, why do GLP-1 RAs consistently demonstrate cardiovascular superiority in trials like LEADER while DPP-4 inhibitors like sitagliptin in TECOS only achieve non-inferiority?

Key Response

DPP-4 inhibitors prevent the breakdown of endogenous GLP-1, only increasing its levels two- to three-fold, which remains within physiological ranges sufficient for glycemic control but insufficient for cardiovascular protection. In contrast, GLP-1 RAs provide pharmacological levels of GLP-1 receptor activation (up to 10-fold higher), which is likely required to drive the anti-atherosclerotic, anti-inflammatory, and weight-loss benefits that translate into MACE reduction.

Attending
Attending

In an era where SGLT2 inhibitors and GLP-1 RAs offer profound cardiovascular and renal benefits, what is the pragmatic clinical rationale for continuing to prescribe sitagliptin given its purely neutral cardiovascular profile demonstrated in TECOS?

Key Response

While sitagliptin lacks the cardioprotective benefits of SGLT2is or GLP-1 RAs, it remains highly valuable in practice for its excellent tolerability profile, low risk of hypoglycemia, weight neutrality, and oral administration. It is particularly useful as an add-on or alternative in frail, elderly patients, those with chronic kidney disease, or patients who cannot tolerate the gastrointestinal side effects of GLP-1 RAs or the genitourinary risks of SGLT2 inhibitors.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

TECOS was designed as a non-inferiority trial with a pre-specified upper bound of the 95% confidence interval for the hazard ratio set at 1.3. How does the inclusion of hospitalization for unstable angina in the primary composite endpoint impact the trial's statistical power and clinical interpretation?

Key Response

The 1.3 margin was an FDA mandate for diabetes CVOTs to confidently rule out unacceptable ischemic risk. Including hospitalization for unstable angina (a 'softer' endpoint compared to hard MACE like CV death or MI) increases the overall event rate, which enhances statistical power and narrows the confidence intervals. However, it can dilute the impact of fatal events and complicate the interpretation of true mortality risk, introducing potential ascertainment bias compared to strictly hard endpoints.

Journal Editor
Journal Editor

A critical requirement for interpreting diabetes cardiovascular outcome trials is achieving 'glycemic equipoise' between the treatment and placebo arms. How did the TECOS investigators manage concurrent glucose-lowering therapies, and what potential threat to validity would occur if the HbA1c significantly diverged?

Key Response

Investigators were encouraged to aggressively adjust background diabetes medications to maintain similar HbA1c levels in both the sitagliptin and placebo arms. If the sitagliptin arm had significantly lower HbA1c, reviewers would question whether any observed CV safety was due to the drug's specific pleiotropic profile or simply better glycemic control. Glycemic equipoise isolates the independent cardiovascular effects of the study drug from the general effects of glucose lowering.

Guideline Committee
Guideline Committee

Current ADA/EASD guidelines heavily prioritize SGLT2 inhibitors and GLP-1 RAs in patients with ASCVD or heart failure. Based on the neutral findings of TECOS, what specific position should sitagliptin occupy in the algorithm for patients who require additional glycemic control but have an established history of heart failure?

Key Response

Current ADA guidelines relegate DPP-4 inhibitors to later-line therapy if cost, patient preference, or tolerability precludes SGLT2i or GLP-1RA use. Because TECOS proved sitagliptin does not increase heart failure risk (unlike the saxagliptin findings in SAVOR-TIMI), the guidelines specifically recommend sitagliptin or linagliptin (Level A evidence) over saxagliptin if a DPP-4 inhibitor must be used in a patient with heart failure, ensuring safety without claiming superiority.

Clinical Landscape

Noteworthy Related Trials

2013

SAVOR-TIMI 53

n = 16,492 · NEJM

Tested

Saxagliptin 5mg daily

Population

T2DM patients with history of, or risk for, cardiovascular events

Comparator

Placebo

Endpoint

3-point MACE

Key result: Saxagliptin did not increase or decrease the rate of ischemic events but significantly increased the risk of hospitalization for heart failure.
2013

EXAMINE Trial

n = 5,380 · NEJM

Tested

Alogliptin

Population

T2DM patients with recent acute coronary syndrome

Comparator

Placebo

Endpoint

3-point MACE

Key result: Alogliptin resulted in rates of major adverse cardiovascular events that were noninferior to placebo.
2015

EMPA-REG OUTCOME

n = 7,020 · NEJM

Tested

Empagliflozin 10mg or 25mg daily

Population

T2DM patients with established cardiovascular disease

Comparator

Placebo

Endpoint

3-point MACE

Key result: Empagliflozin significantly reduced the risk of the primary composite outcome and cardiovascular death compared to placebo.

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