New England Journal of Medicine MARCH 03, 2022

Nirsevimab for Prevention of RSV in Healthy Late-Preterm and Term Infants

Hammitt LL, Dagan R, Yuan Y, et al. (MELODY Study Group)

Bottom Line

A single intramuscular dose of the long-acting monoclonal antibody nirsevimab significantly reduced the incidence of medically attended lower respiratory tract infections caused by respiratory syncytial virus in healthy term and late-preterm infants.

Key Findings

1. Nirsevimab demonstrated a 74.5% efficacy (95% CI, 49.6 to 87.1; P<0.001) in preventing medically attended RSV-associated lower respiratory tract infection (LRTI) through 150 days post-dose, with an event rate of 1.2% in the nirsevimab group versus 5.0% in the placebo group.
2. The secondary endpoint of hospitalization for RSV-associated LRTI showed an efficacy of 62.1% (95% CI, -8.6 to 86.8; P=0.07), with event rates of 0.6% in the nirsevimab group and 1.6% in the placebo group.
3. Safety outcomes were comparable between groups, with serious adverse events reported in 6.8% of infants in the nirsevimab group and 7.3% in the placebo group, suggesting a favorable safety profile.
4. The extended half-life of nirsevimab allows for single-dose protection throughout the entire typical RSV season.

Study Design

Design
RCT
Double-Blind
Sample
1,490
Patients
Duration
150 days
Median
Setting
Multicenter, international
Population Healthy infants born at a gestational age of at least 35 weeks, entering their first RSV season
Intervention Single intramuscular injection of nirsevimab (weight-banded dosing: 50 mg if <5 kg, 100 mg if ≥5 kg)
Comparator Placebo
Outcome Medically attended RSV-associated lower respiratory tract infection through 150 days after the injection

Study Limitations

The study was not sufficiently powered to reach statistical significance for the secondary outcome of hospitalization for RSV-associated LRTI.
The trial was conducted during periods affected by the COVID-19 pandemic, which may have influenced RSV circulation patterns and healthcare-seeking behaviors.
While statistically significant for the primary endpoint, the confidence intervals for efficacy are relatively broad, reflecting the low absolute event rates.
The trial excluded infants born at less than 35 weeks gestational age, limiting direct generalizability to the most vulnerable preterm populations.

Clinical Significance

Nirsevimab represents a paradigm shift in RSV prevention, offering a simple, single-dose monoclonal antibody option for the general infant population, potentially replacing or augmenting existing high-risk-only prophylaxis regimens like palivizumab.

Historical Context

For decades, RSV prevention was limited to high-risk infants via monthly injections of palivizumab. The development of nirsevimab, an extended half-life monoclonal antibody targeting the prefusion F protein, addresses the long-standing need for a practical, season-long preventative measure for all infants.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

Explain the pharmacological mechanism that allows nirsevimab to be administered as a single dose for the entire RSV season, whereas palivizumab requires monthly injections.

Key Response

Nirsevimab is a monoclonal antibody targeting the prefusion conformation of the RSV fusion (F) protein. It features a triple amino acid substitution (YTE) in the Fc region, which increases its affinity for the neonatal Fc receptor (FcRn). This enhancement promotes the recycling of the antibody back into the circulation rather than degradation, extending its half-life to approximately 60 to 70 days, which is significantly longer than the 20-day half-life of palivizumab.

Resident
Resident

In a healthy term infant presenting during their first RSV season, how do the results of the MELODY trial regarding 'medically attended lower respiratory tract infection' (MALRTI) influence your counseling on the benefits of nirsevimab compared to supportive care alone?

Key Response

The MELODY trial showed that nirsevimab reduced the incidence of RSV-associated MALRTI by 74.5% compared to placebo. Residents should be able to explain to parents that while most RSV is mild, this intervention significantly lowers the risk of the child needing a clinic or emergency room visit, effectively shifting the burden of disease away from the outpatient and acute care settings during peak season.

Fellow
Fellow

The MELODY trial utilized a primary endpoint of medically attended LRTI. Discuss the clinical and immunological implications of 'breakthrough' infections observed in the nirsevimab group—specifically, do these represent a failure of neutralization or an expected decay in antibody titers over the 150-day observation period?

Key Response

Fellows must integrate pharmacokinetic data with clinical outcomes. Breakthroughs may occur if the viral inoculum overcomes the passive antibody concentration or if mutations occur at the highly conserved site &Oslash; on the F protein. Analysis of the trial data suggests that protection remains high throughout the 150-day period, suggesting that most breakthroughs are likely due to host factors or high-exposure events rather than a rapid loss of therapeutic levels.

Attending
Attending

The MELODY trial demonstrates efficacy in healthy infants, who represent the largest absolute number of RSV hospitalizations. How does this shift the traditional 'high-risk' prophylaxis paradigm, and what are the teaching points for trainees regarding the difference between passive immunization and active vaccination?

Key Response

Historically, RSV prophylaxis was restricted to high-risk groups (preterm, CHD, CLD) due to the costs of palivizumab. Nirsevimab moves the strategy toward universal prevention. Attendings should teach that nirsevimab provides immediate 'passive' immunity (pre-formed antibodies), which is distinct from 'active' vaccination (inducing the infant's own immune response), making it an ideal strategy for neonates with immature immune systems entering their first viral season.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

Critique the statistical handling of the 'primary pool' analysis in the MELODY trial, which was necessitated by the COVID-19 pandemic. How might the disruption of normal RSV seasonality during the study period affect the generalizability of the reported efficacy and the calculation of the absolute risk reduction?

Key Response

The pandemic led to a period of near-zero RSV circulation, causing a hiatus in enrollment. The researchers analyzed a 'primary pool' of infants enrolled before the hiatus. A PhD researcher would note that if RSV seasons post-pandemic are more or less severe, the Absolute Risk Reduction (ARR) and Number Needed to Treat (NNT) observed in the trial may fluctuate, even if the Relative Risk Reduction (RRR) remains stable, impacting future cost-effectiveness models.

Journal Editor
Journal Editor

As a reviewer, evaluate the potential for 'diagnostic overshadowing' or bias in the MELODY trial's secondary endpoint of hospitalization. Since the study was double-blinded, could the reduction in medically attended visits have indirectly influenced the rate of hospitalization by altering the threshold for physician referral?

Key Response

Editors look for subtle biases. If a clinician knows an infant is part of an RSV prevention trial, they might monitor them more closely or differently. However, because the trial was robustly double-blinded, the reduction in hospitalizations (62.1% in the primary pool) likely reflects a true reduction in disease severity. A tough reviewer would scrutinize whether the criteria for 'hospitalization' were standardized across international study sites to ensure the endpoint's validity.

Guideline Committee
Guideline Committee

How does the evidence from the MELODY trial support a change in the AAP Red Book recommendations from a targeted approach (palivizumab for <29 weeks GA) to a universal approach (nirsevimab for all infants)? What specific evidence gaps remain regarding long-term safety?

Key Response

The MELODY trial provided high-quality (Level 1) evidence for healthy infants ≥35 weeks GA. Combined with the MEDLEY trial (comparing nirsevimab to palivizumab in high-risk infants), the data supports the ACIP/AAP recommendation for a single dose for all infants <8 months. The committee must consider that while efficacy is clear, ongoing surveillance is required to monitor for rare adverse events and the potential emergence of RSV variants that could escape neutralization.

Clinical Landscape

Noteworthy Related Trials

1998

IMpact-RSV Trial

n = 1502 · NEJM

Tested

Palivizumab

Population

Preterm infants and children with chronic lung disease

Comparator

Placebo

Endpoint

RSV-related hospitalization

Key result: Palivizumab treatment resulted in a 55 percent reduction in RSV-related hospitalizations compared to placebo.
2021

MEDLEY Trial

n = 925 · JAMA

Tested

Nirsevimab

Population

Preterm infants and infants with chronic lung disease or hemodynamically significant congenital heart disease

Comparator

Palivizumab

Endpoint

Safety and serum concentration of nirsevimab

Key result: Nirsevimab demonstrated a safety profile similar to palivizumab with comparable serum concentrations during the RSV season.
2023

PROTECT Trial

n = 1490 · NEJM

Tested

Nirsevimab

Population

Healthy preterm and term infants

Comparator

Placebo

Endpoint

Medically attended RSV-associated lower respiratory tract infection

Key result: Nirsevimab efficacy was confirmed in reducing medically attended RSV lower respiratory tract infections in healthy infants through 150 days post-dose.

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