New England Journal of Medicine SEPTEMBER 18, 2014

Withdrawal of Inhaled Corticosteroids and Exacerbations of COPD (WISDOM)

Magnussen H, Watz H, Kirsten A, et al.

Bottom Line

In patients with severe to very severe COPD receiving triple therapy, stepwise withdrawal of inhaled corticosteroids did not significantly increase the risk of moderate or severe exacerbations compared with continuing triple therapy over 52 weeks.

Key Findings

1. Stepwise withdrawal of inhaled corticosteroids was non-inferior to continuation regarding the time to first moderate or severe exacerbation (hazard ratio 1.06; 95% CI 0.94–1.19; P=0.35).
2. The rate of moderate or severe exacerbations was not statistically different between the withdrawal and continuation groups (rate ratio 1.04; 95% CI 0.92–1.18).
3. Patients in the withdrawal group experienced a small but statistically significant decline in trough FEV1 compared with those continuing ICS (adjusted mean difference of 38 mL, P<0.0001).
4. Post-hoc analyses identified that patients with higher baseline blood eosinophil counts (e.g., ≥4% or ≥5%) are at increased risk of exacerbations following ICS withdrawal compared to continuation.

Study Design

Design
RCT
Double-Blind
Sample
2,485
Patients
Duration
52 wk
Median
Setting
Multicenter, International
Population Patients with severe or very severe COPD (GOLD stage 3 or 4) and a history of at least one exacerbation in the 12 months prior to screening.
Intervention Stepwise withdrawal of inhaled corticosteroids over 12 weeks while continuing dual bronchodilators (tiotropium and salmeterol).
Comparator Continuation of triple therapy (tiotropium, salmeterol, and fluticasone).
Outcome Time to the first moderate or severe COPD exacerbation.

Study Limitations

The study focused on patients with severe to very severe COPD (GOLD 3-4) and a history of exacerbations, potentially limiting generalizability to patients with milder disease.
The 12-week stepwise withdrawal process may mask acute rebound effects that could occur with abrupt cessation.
The trial was not powered to detect differences in mortality or long-term safety endpoints like pneumonia risk.
Subgroup findings regarding blood eosinophil counts are post-hoc and require prospective validation.

Clinical Significance

The WISDOM trial challenged the dogma that all patients with severe COPD and a history of exacerbations require continuous inhaled corticosteroid therapy, suggesting that ICS can be withdrawn in many patients without increasing moderate-to-severe exacerbation risk, provided they are maintained on dual bronchodilator therapy. However, the potential for a small decline in lung function and increased risk in eosinophilic patients necessitates a personalized, risk-based approach to ICS withdrawal.

Historical Context

Prior to WISDOM, clinical guidelines heavily favored the inclusion of inhaled corticosteroids in the maintenance therapy of patients with severe COPD and frequent exacerbations. This trial was a landmark study that initiated a paradigm shift toward questioning the overuse of ICS, which carries risks of adverse effects like pneumonia, and promoting dual bronchodilation as the backbone of COPD management.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

Why is the role of inhaled corticosteroids (ICS) in the management of COPD considered fundamentally different from their role in asthma, particularly regarding the underlying cellular inflammatory profile?

Key Response

In asthma, the inflammation is typically eosinophilic and Th2-driven, which is highly responsive to steroids. In contrast, COPD inflammation is primarily neutrophilic and Th1-driven, which is relatively steroid-resistant. The WISDOM trial tests the hypothesis that because this underlying inflammation is less responsive, the ICS component of triple therapy may be redundant in certain COPD phenotypes.

Resident
Resident

In a patient with severe COPD currently stable on triple therapy (ICS/LABA/LAMA), what specific clinical factors from the WISDOM trial results should guide your decision to attempt a stepwise withdrawal of the ICS component?

Key Response

The WISDOM trial suggests that in patients with severe to very severe airflow limitation who are stable on long-acting dual bronchodilators (LABA/LAMA), ICS can be withdrawn without increasing the risk of moderate-to-severe exacerbations. However, clinicians should monitor for a potential slight decline in FEV1 and consider the patient's individual history of exacerbations and pneumonia risk before proceeding.

Fellow
Fellow

Post-hoc analyses of the WISDOM trial identified a specific biomarker threshold that predicted a higher risk of exacerbations upon ICS withdrawal; how does this finding reconcile the trial's primary non-inferiority result with the concept of 'ICS-responsive' COPD phenotypes?

Key Response

While the primary trial met non-inferiority for the overall population, subsequent analysis showed that patients with blood eosinophil counts ≥300 cells/µL experienced a significant increase in exacerbation frequency after ICS withdrawal. This indicates that the 'non-inferiority' observed was an average effect, and that precision medicine using eosinophils is necessary to identify the subset of COPD patients who derive true benefit from ICS.

Attending
Attending

Given that the WISDOM trial demonstrated a statistically significant (though small) decrease in FEV1 following ICS withdrawal, how do you balance this physiological decline against the reduction in long-term steroid-related adverse effects when teaching de-escalation strategies?

Key Response

The withdrawal group saw an FEV1 decline of approximately 38-43 mL. While statistically significant, this is often considered below the threshold of clinical importance for an individual patient. Attendings should teach that for many patients, avoiding the increased risk of pneumonia, oral candidiasis, and bone density loss associated with long-term ICS use outweighs the minor physiological loss in lung function.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

The WISDOM trial utilized a 'stepwise' withdrawal of ICS over 12 weeks rather than abrupt cessation; what are the methodological implications of this tapering design on the trial's ability to detect a rebound inflammatory effect or acute treatment failure?

Key Response

Stepwise withdrawal minimizes the risk of an acute 'rebound' effect by allowing the airway's homeostatic mechanisms to adjust. While this increases the safety and clinical relevance of the trial (mimicking real-world practice), it potentially masks more immediate ICS-dependency signals that an abrupt cessation design might have revealed, thus potentially biasing the results toward non-inferiority.

Journal Editor
Journal Editor

A critical reviewer might argue that the WISDOM trial's non-inferiority margin of 1.20 for the hazard ratio was too permissive; how does the choice of this margin influence the interpretation of 'safety' in the context of a drug withdrawal study?

Key Response

In non-inferiority trials, the margin represents the maximum acceptable loss of efficacy. A margin of 1.20 means the study could conclude 'non-inferiority' even if the withdrawal group had a 20% higher risk of exacerbations. As an editor, one must weigh whether a 20% increased risk is clinically acceptable for a 'stable' patient, especially when the intervention is the removal of a standard-of-care medication.

Guideline Committee
Guideline Committee

How do the results of the WISDOM trial, in conjunction with the SUNSET study, inform the current GOLD (Global Initiative for Chronic Obstructive Lung Disease) recommendations regarding 'de-escalation' of therapy?

Key Response

The WISDOM trial provides the evidence base for GOLD's current stance that ICS withdrawal is feasible in stable patients on dual bronchodilation, provided they do not have high blood eosinophils (typically <300 cells/µL) or a history of frequent exacerbations. It shifted the guidelines from a 'escalation-only' mindset to a dynamic approach where therapy is tailored to the patient's current risk-benefit profile, specifically recommending caution in withdrawal for those with an eosinophilic phenotype.

Clinical Landscape

Noteworthy Related Trials

2007

TORCH Trial

n = 6,112 · NEJM

Tested

Salmeterol/Fluticasone propionate combination

Population

Patients with moderate-to-severe COPD

Comparator

Placebo, Salmeterol alone, and Fluticasone propionate alone

Endpoint

All-cause mortality

Key result: The combination therapy reduced the rate of exacerbations and improved lung function compared to placebo, although the mortality benefit did not reach statistical significance.
2014

OPTIMAL Trial

n = 1,100 · Lancet Respir Med

Tested

Withdrawal of inhaled corticosteroids

Population

Patients with stable COPD receiving triple therapy

Comparator

Continued triple therapy

Endpoint

Time to first moderate or severe exacerbation

Key result: Withdrawal of inhaled corticosteroids did not result in a significant increase in exacerbations in patients who were clinically stable.
2016

FLAME Trial

n = 3,362 · NEJM

Tested

Indacaterol/Glycopyrronium dual bronchodilation

Population

Patients with COPD and a history of exacerbations

Comparator

Salmeterol/Fluticasone

Endpoint

Annual rate of all COPD exacerbations

Key result: Dual bronchodilation was superior to inhaled corticosteroid-based combination therapy in reducing the rate of exacerbations.

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