The New England Journal of Medicine October 02, 2014

Withdrawal of Inhaled Glucocorticoids and Exacerbations of COPD (WISDOM)

Helgo Magnussen, Bernd Disse, Roberto Rodriguez-Roisin, et al.

Bottom Line

In patients with severe COPD, the stepwise withdrawal of inhaled glucocorticoids while continuing dual bronchodilator therapy did not increase the risk of moderate or severe exacerbations, though it led to a small decrease in lung function.

Key Findings

1. The hazard ratio for the time to first moderate or severe COPD exacerbation was 1.06 (95% CI, 0.94 to 1.19) for the ICS-withdrawal group compared to the continuation group, satisfying the prespecified noninferiority limit of 1.20.
2. At week 18, when glucocorticoid withdrawal was complete, the adjusted mean reduction from baseline in trough FEV1 was 38 mL greater in the withdrawal group than in the continuation group (P<0.001).
3. At week 52, the decline in lung function persisted, with the trough FEV1 being 43 mL lower in the withdrawal group compared to the continuation arm (P=0.001).
4. There were no significant differences in adverse events, health status (St. George's Respiratory Questionnaire scores), or dyspnea between the two treatment groups over the 52-week period.

Study Design

Design
RCT
Double-Blind
Sample
2,485
Patients
Duration
52 wk
Median
Setting
Multicenter, global
Population Patients aged 40 or older with severe or very severe COPD (FEV1 <50% of predicted) and a documented history of at least one exacerbation in the previous 12 months.
Intervention Stepwise withdrawal of the inhaled glucocorticoid fluticasone propionate (reduced from 500 μg twice daily down to zero over a 12-week period) while continuing maintenance tiotropium (18 μg once daily) and salmeterol (50 μg twice daily).
Comparator Continuation of triple therapy with tiotropium (18 μg once daily), salmeterol (50 μg twice daily), and fluticasone propionate (500 μg twice daily).
Outcome Time to the first moderate or severe COPD exacerbation.

Study Limitations

Although the 43 mL reduction in FEV1 was below standard thresholds for clinical relevance on a population level, it could be clinically significant for individual patients with very severe baseline impairment.
The study was not prospectively stratified by blood eosinophil counts; subsequent post-hoc analyses indicated that patients with elevated eosinophils experienced increased exacerbation risk upon ICS withdrawal.
The prespecified noninferiority margin for the hazard ratio (upper limit of 1.20) was relatively wide, and the 52-week follow-up may not have fully captured the long-term clinical trajectory of the observed FEV1 decline.

Clinical Significance

The WISDOM trial challenged the longstanding practice of indefinite inhaled corticosteroid (ICS) use for all patients with severe COPD. By demonstrating that ICS could be safely de-escalated in patients receiving optimal dual long-acting bronchodilator therapy (LABA/LAMA) without increasing the risk of exacerbations, the trial provided a framework to reduce the long-term adverse effects of ICS, such as pneumonia and bone density loss. It laid the foundation for modern personalized COPD management, wherein ICS therapy is targeted primarily to patients with specific traits, such as elevated blood eosinophils or a history of recurrent exacerbations despite maximal bronchodilation.

Historical Context

Prior to 2014, clinical guidelines broadly recommended the addition of inhaled corticosteroids to bronchodilators for patients with severe COPD and a history of frequent exacerbations. However, as evidence grew regarding the efficacy of combined long-acting beta-agonists (LABA) and long-acting muscarinic antagonists (LAMA) in preventing exacerbations, the additive value of ICS became questionable. Simultaneously, concerns were mounting over the well-documented side effects of prolonged ICS use in older adults. The WISDOM trial was designed to formally investigate whether de-prescribing ICS in the context of robust dual bronchodilator therapy was a safe and viable strategy.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

What is the pathophysiological rationale for using inhaled corticosteroids in COPD, and how does the underlying inflammation in COPD differ from that in asthma, potentially explaining the findings of the WISDOM trial?

Key Response

Asthma is typically characterized by eosinophilic, Th2-driven inflammation which is highly responsive to corticosteroids. In contrast, COPD is predominantly driven by neutrophilic, CD8+ T-cell, and macrophage-mediated inflammation triggered by irritants like smoking, which is relatively corticosteroid-resistant. This fundamental difference explains why stepping down ICS in COPD may not significantly worsen exacerbation risk, whereas it would be detrimental in asthma.

Resident
Resident

A patient with severe COPD is currently stable on triple therapy (ICS/LABA/LAMA). Based on the WISDOM trial, you consider withdrawing the ICS. What specific adverse effects of long-term ICS use justify this de-escalation, and what parameters should you monitor during the withdrawal process?

Key Response

Long-term ICS use in COPD is associated with an increased risk of pneumonia, oral candidiasis, osteoporosis, skin bruising, and potentially mycobacterial infections. The WISDOM trial demonstrated that ICS can be withdrawn without increasing exacerbation risk, but since there was a minor drop in FEV1, clinicians should monitor spirometry and symptoms to ensure the patient tolerates the transition to dual bronchodilator therapy.

Fellow
Fellow

Post-hoc analyses of the WISDOM trial and subsequent studies emphasize the role of peripheral blood eosinophils. How does the blood eosinophil count modify the risk of exacerbation upon ICS withdrawal, and how should a pulmonologist use this biomarker to select candidates for ICS de-escalation?

Key Response

Subsequent analyses showed that patients with higher blood eosinophil counts (e.g., greater than or equal to 300 cells/microL) are at a higher risk of exacerbation if ICS is withdrawn. Pulmonologists use eosinophil counts as a biomarker for Th2-mediated inflammation in COPD; patients with high counts benefit from continued ICS, whereas those with low counts are ideal candidates for ICS withdrawal.

Attending
Attending

The WISDOM trial revealed a statistically significant decline in FEV1 after ICS withdrawal, yet no increase in exacerbations. How do you reconcile discordant FEV1 and exacerbation outcomes when counseling patients and junior trainees about the clinical meaning of 'stability' in COPD?

Key Response

FEV1 is a surrogate physiological marker that does not perfectly correlate with clinical outcomes like exacerbation frequency, dyspnea, or quality of life in COPD. The trial teaches that a marginal drop in FEV1 (about 43 mL) may not be clinically relevant or translate to increased exacerbations when patients are covered by dual bronchodilation. We must treat the patient's clinical risk, not just the spirometry numbers.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

The WISDOM trial utilized a non-inferiority design for its primary endpoint. What are the methodological challenges in defining the non-inferiority margin for COPD exacerbations, and how might the 'stepwise' withdrawal design introduce bias compared to an abrupt cessation model?

Key Response

Selecting a non-inferiority margin requires balancing statistical feasibility with clinical relevance (WISDOM used a hazard ratio upper bound of 1.20). Methodologically, a stepwise withdrawal mimics clinical practice but complicates the isolation of the exact time point when drug withdrawal effects occur, potentially delaying the observation of exacerbations due to a prolonged washout period, thus biasing the results toward non-inferiority.

Journal Editor
Journal Editor

As a peer reviewer, how would you critically evaluate the generalizability of the WISDOM trial given that all patients underwent a 6-week run-in period on triple therapy before randomization, and how might this 'enrichment' strategy mask the true effect of ICS withdrawal in a real-world unselected population?

Key Response

The run-in period stabilizes all patients on triple therapy, ensuring compliance but also potentially selecting for a cohort that is inherently stable and responsive. A tough reviewer would flag that withdrawing ICS in patients who have been artificially stabilized might underestimate the withdrawal risks compared to real-world patients who have fluctuating adherence or distinct exacerbation phenotypes not captured by the inclusion criteria.

Guideline Committee
Guideline Committee

How do the findings of the WISDOM trial influence the GOLD (Global Initiative for Chronic Obstructive Lung Disease) guideline recommendations regarding the de-escalation of triple therapy, specifically concerning the strength of recommendation for using LABA/LAMA combinations over continued ICS use?

Key Response

The WISDOM trial provided pivotal evidence for GOLD guidelines to recommend ICS withdrawal (stepping down to LABA/LAMA) in patients without frequent exacerbations and low eosinophils. Current GOLD guidelines support de-escalation for patients who lack asthma history and have eosinophils less than 300 cells/microL to mitigate pneumonia risk. The trial supports a strong recommendation for dual bronchodilator maintenance as sufficient for exacerbation prevention in this specific low-eosinophil phenotype.

Clinical Landscape

Noteworthy Related Trials

2007

TORCH Trial

n = 6,112 · NEJM

Tested

Salmeterol/fluticasone (LABA/ICS)

Population

Patients with moderate-to-severe COPD

Comparator

Placebo, salmeterol alone, or fluticasone alone

Endpoint

All-cause mortality at 3 years

Key result: LABA/ICS did not significantly reduce all-cause mortality compared to placebo but did significantly reduce exacerbation rates and improve lung function.
2016

FLAME Trial

n = 3,362 · NEJM

Tested

Indacaterol/glycopyrronium (LABA/LAMA)

Population

COPD patients with at least 1 exacerbation in the previous year

Comparator

Salmeterol/fluticasone (LABA/ICS)

Endpoint

Annual rate of all COPD exacerbations

Key result: LABA/LAMA was superior to LABA/ICS in preventing COPD exacerbations.
2018

IMPACT Trial

n = 10,355 · NEJM

Tested

Fluticasone furoate/umeclidinium/vilanterol (ICS/LAMA/LABA)

Population

Symptomatic COPD patients with a history of exacerbations

Comparator

ICS/LABA or LAMA/LABA

Endpoint

Annual rate of moderate or severe COPD exacerbations

Key result: Triple therapy resulted in a significantly lower rate of moderate or severe COPD exacerbations than either dual therapy.

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