The Lancet AUGUST 15, 2009

Percutaneous closure of the left atrial appendage versus warfarin therapy for prevention of stroke in patients with atrial fibrillation (PROTECT AF)

Holmes DR Jr, Reddy VY, Turi ZG, Doshi SK, Sievert H, Buchbinder M, Mullin CM, Sick P, Aeschbacher BC, for the PROTECT AF Investigators

Bottom Line

The PROTECT AF trial demonstrated that percutaneous left atrial appendage closure with the Watchman device was noninferior to long-term warfarin therapy for the prevention of stroke, systemic embolism, and cardiovascular death in patients with nonvalvular atrial fibrillation.

Key Findings

1. The primary composite efficacy endpoint (stroke, systemic embolism, or cardiovascular/unexplained death) occurred at a rate of 3.0 per 100 patient-years in the device group versus 4.9 per 100 patient-years in the warfarin group, confirming noninferiority (posterior probability >99.9%).
2. The primary safety endpoint (bleeding-related or procedure-related complications) was higher in the device group (7.4 per 100 patient-years) compared to the warfarin control group (4.4 per 100 patient-years), largely driven by procedure-related pericardial effusions.
3. Long-term follow-up suggested that once the short-term procedural risk was overcome, the device strategy provided robust stroke prophylaxis, with secondary analyses even suggesting superiority over warfarin after discontinuation of short-term antithrombotic therapy.

Study Design

Design
RCT
Open-Label
Sample
707
Patients
Duration
2.3 yr
Median
Setting
Multicenter, Global
Population Patients with nonvalvular atrial fibrillation and at least one risk factor (CHADS2 score ≥1) eligible for long-term warfarin therapy.
Intervention Percutaneous left atrial appendage closure with the Watchman device, followed by 45 days of warfarin and subsequent transition to antiplatelet therapy.
Comparator Long-term dose-adjusted warfarin therapy (target INR 2.0–3.0).
Outcome Composite of stroke (ischemic or hemorrhagic), systemic embolism, or cardiovascular/unexplained death.

Study Limitations

The trial observed a higher rate of acute procedure-related complications in the intervention arm compared to long-term systemic anticoagulation.
The study was open-label, which could introduce bias in the reporting of outcomes, although the primary endpoint was composite and included objective clinical events.
The noninferiority margin was relatively broad, which generated debate regarding the clinical threshold for accepting device-related procedural risks.
The trial was conducted early in the development of the device, and procedural safety has likely improved with operator experience in subsequent years.

Clinical Significance

PROTECT AF established the left atrial appendage as a critical source of thromboemboli in nonvalvular atrial fibrillation, providing the first major randomized evidence that a mechanical, device-based 'local' strategy could serve as a viable alternative to lifelong systemic anticoagulation.

Historical Context

Before PROTECT AF, systemic vitamin K antagonists like warfarin were the standard of care for stroke prevention in atrial fibrillation despite significant limitations regarding patient adherence, monitoring, and bleeding risks. This trial was seminal in shifting the paradigm toward percutaneous structural heart interventions for stroke prophylaxis.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

What is the anatomical and pathophysiological rationale for targeting the left atrial appendage (LAA) specifically in patients with non-valvular atrial fibrillation to prevent embolic stroke?

Key Response

In patients with non-valvular atrial fibrillation (AF), approximately 90% of thrombi that cause embolic strokes originate in the left atrial appendage due to its pouch-like structure and stasis during AF. Mechanically occluding or excluding the LAA eliminates the primary site of clot formation, theoretically offering a localized alternative to systemic anticoagulation.

Resident
Resident

The PROTECT AF trial showed a 'front-loaded' risk profile for the Watchman device. How should a clinician counsel a patient on the trade-off between the early procedural risks and the long-term benefits compared to chronic warfarin therapy?

Key Response

PROTECT AF demonstrated a high initial rate of serious adverse events (10.6%), primarily procedure-related complications like pericardial effusion and device embolization. However, over long-term follow-up, the device group had lower rates of hemorrhagic stroke and cardiovascular death. Counseling must emphasize that the device carries higher immediate risk to achieve a long-term reduction in bleeding and mortality compared to lifelong anticoagulation.

Fellow
Fellow

In the PROTECT AF protocol, patients were required to take warfarin for 45 days post-implantation. How does this requirement impact the clinical decision-making for patients who are referred for LAA closure specifically because they have a high risk of bleeding on oral anticoagulants?

Key Response

Because PROTECT AF included only patients eligible for warfarin, its results technically only apply to that cohort. For patients with absolute contraindications to anticoagulation, the 45-day warfarin bridge is a major barrier. This led to subsequent studies like the ASAP trial, which explored the safety of using DAPT post-implant for those unable to tolerate even short-term warfarin.

Attending
Attending

PROTECT AF eventually showed a survival benefit in long-term follow-up. Given that modern practice has shifted from warfarin to DOACs, how does the 'legacy' evidence from PROTECT AF hold up when discussing LAA closure as a primary alternative to DOAC therapy today?

Key Response

While PROTECT AF proved non-inferiority and eventual superiority to warfarin, warfarin is no longer the gold standard. DOACs have better safety profiles (lower intracranial hemorrhage) than warfarin. Therefore, the survival benefit seen in PROTECT AF might be less pronounced if the comparator were a DOAC, necessitating a more nuanced discussion about the lack of large-scale head-to-head randomized trials between Watchman and DOACs (e.g., OPTION or CHAMPION-AF trials).

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

The PROTECT AF trial utilized a Bayesian statistical design to evaluate non-inferiority. What are the methodological advantages and potential pitfalls of using a Bayesian approach with a non-inferiority margin of 2.0 for the rate ratio in this specific device-versus-drug comparison?

Key Response

The Bayesian approach allows for the integration of accumulating data to calculate the probability of non-inferiority, which is useful for complex device trials. However, a non-inferiority margin of 2.0 is relatively lax (allowing the device to potentially be twice as bad as the drug), which was criticized. Critics argued this margin was chosen due to the small sample size and expected event rates rather than purely clinical equivalence.

Journal Editor
Journal Editor

The PROTECT AF results were initially met with skepticism by the FDA and peer reviewers due to the high rate of complications in the intervention arm. From an editorial standpoint, how should the 'learning curve' of a new interventional technology be weighted when evaluating the safety endpoints of a pivotal trial?

Key Response

Editors must distinguish between inherent device failure and operator-dependent complications. In PROTECT AF, the rate of pericardial effusion decreased significantly as the trial progressed and operators gained experience. An editor looks for whether the 'learning curve' is documented and if the results are generalizable to real-world centers that may not have the same volume or expertise as the trial sites.

Guideline Committee
Guideline Committee

The 2023 ACC/AHA/ACCP/HRS AF guidelines provide a Class 2b recommendation for LAA closure in patients with contraindications to long-term OAC. Based on PROTECT AF and PREVAIL, why has the evidence not reached a Class 1 recommendation level for patients who are otherwise good candidates for anticoagulation?

Key Response

Current guidelines (Class 2b) reflect that while LAA closure is effective, the primary trials (PROTECT AF, PREVAIL) compared it to warfarin, not modern DOACs. Additionally, the procedure carries a risk of major complications (3-4%). For a Class 1 recommendation, the committee would require more robust, contemporary head-to-head data against DOACs showing either superior safety or equivalent long-term stroke prevention without the 'front-loaded' procedural morbidity.

Clinical Landscape

Noteworthy Related Trials

2014

PREVAIL Trial

n = 407 · JACC

Tested

Watchman LAA closure device

Population

Patients with non-valvular AF at risk for stroke

Comparator

Warfarin

Endpoint

Composite of stroke, systemic embolism, cardiovascular death, or unexplained death

Key result: The study did not meet the criteria for non-inferiority regarding the composite primary endpoint, though it demonstrated safety outcomes consistent with PROTECT AF.
2017

ST-WATCHMAN Trial

n = 3822 · J Am Heart Assoc

Tested

Watchman LAA closure device

Population

Non-valvular AF patients with contraindications to oral anticoagulation

Comparator

Standard of care (often antiplatelet therapy)

Endpoint

Incidence of ischemic stroke or systemic embolism

Key result: Real-world registry data showed low rates of stroke and procedure-related complications, supporting the use of LAA closure in patients who cannot tolerate long-term anticoagulation.
2020

CLOSE-UP

n = 1025 · Eur Heart J

Tested

Watchman LAA closure device

Population

Patients with non-valvular AF and high stroke/bleeding risk

Comparator

No intervention (control historical cohorts)

Endpoint

All-cause mortality and stroke

Key result: Pooled analysis showed a significant reduction in stroke and bleeding compared to historical controls not receiving anticoagulation.

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