The New England Journal of Medicine May 23, 2019

Early Neuromuscular Blockade in the Acute Respiratory Distress Syndrome

Marc Moss, David T. Huang, Roy G. Brower, et al. (National Heart, Lung, and Blood Institute PETAL Clinical Trials Network)

Bottom Line

In patients with moderate-to-severe ARDS, early and continuous neuromuscular blockade combined with deep sedation did not significantly reduce 90-day mortality compared to a usual-care strategy of light sedation targets and high PEEP without routine paralysis.

Key Findings

1. At 90 days, all-cause mortality was 42.5% (213 of 501 patients) in the early neuromuscular blockade group compared to 42.8% (216 of 505 patients) in the control group (between-group difference, -0.3 percentage points; 95% CI, -6.4 to 5.9; P = 0.93) [1.2.5].
2. Patients in the intervention group experienced significantly more serious cardiovascular adverse events than the usual-care group.
3. There was no significant difference in the incidence of ICU-acquired weakness at day 28 between the two groups, though patients in the continuous blockade arm were less physically active while hospitalized.
4. The trial was terminated early for futility at the second interim analysis.

Study Design

Design
RCT
Open-Label
Sample
1,006
Patients
Duration
90 days
Median
Setting
Multicenter, US
Population Adults mechanically ventilated for moderate-to-severe ARDS (PaO2/FiO2 <150 mm Hg) enrolled within 48 hours of meeting criteria.
Intervention Continuous intravenous infusion of cisatracurium for 48 hours accompanied by deep sedation.
Comparator Usual care featuring light sedation targets without routine neuromuscular blockade.
Outcome All-cause mortality at 90 days before hospital discharge.

Study Limitations

The trial was unblinded, which could introduce performance and detection bias regarding co-interventions such as fluid management, prone positioning, or decisions to withdraw life support.
A considerable minority (17%) of patients in the control group eventually required some use of neuromuscular blocking agents for refractory hypoxemia or severe dyssynchrony.
The mandated high positive end-expiratory pressure (PEEP) strategy for all patients may have limited the observed benefits of paralysis if one of the mechanisms of paralysis is mitigating atelectrauma.

Clinical Significance

The ROSE trial drove a major paradigm shift away from the routine use of early continuous paralytics in all patients with moderate-to-severe ARDS. It demonstrated that prioritizing light sedation and spontaneous breathing is safe and preferable for the majority of these patients, relegating the use of neuromuscular blockade to rescue therapy for severe patient-ventilator dyssynchrony or refractory hypoxemia.

Historical Context

In 2010, the landmark ACURASYS trial demonstrated a significant 90-day mortality benefit when using continuous cisatracurium for 48 hours in severe ARDS. However, that trial deeply sedated its control arm, which conflicted with the growing consensus over the subsequent decade that light, goal-directed sedation improves ICU outcomes. The ROSE trial (Reevaluation of Systemic Early Neuromuscular Blockade) was designed to compare this paralytic strategy against a modernized control arm using light sedation targets and a high-PEEP ventilation protocol, ultimately showing no benefit to routine paralysis and superseding ACURASYS for standard ARDS management.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

How does early neuromuscular blockade theoretically improve oxygenation and lung mechanics in severe ARDS, and what are the primary physiological risks associated with its use?

Key Response

Tests foundational knowledge of patient-ventilator synchrony, prevention of barotrauma and volutrauma, and reduction in oxygen consumption, balanced against the risks of ICU-acquired weakness, deep vein thrombosis, and hypotension from required deep sedation.

Resident
Resident

Given the conflicting mortality outcomes between the ACURASYS and ROSE trials, under what specific clinical scenarios is the initiation of a neuromuscular blocking agent still indicated for a patient with severe ARDS?

Key Response

Evaluates clinical decision-making. While ROSE showed no benefit for routine use, paralysis remains a vital rescue therapy for refractory hypoxemia, severe patient-ventilator dyssynchrony, or to facilitate prone positioning.

Fellow
Fellow

The ROSE trial utilized a high PEEP strategy and lighter sedation targets in the control arm, differing significantly from the ACURASYS trial. How do these differing ventilator and sedation strategies explain the divergent mortality outcomes between the two studies?

Key Response

Probes nuanced trial interpretation. High PEEP in ROSE may have mitigated the oxygenation benefits of paralysis seen in ACURASYS, while the mandatory deep sedation in the ROSE intervention arm likely contributed to increased cardiovascular adverse events, negating potential benefits.

Attending
Attending

How do the findings of the ROSE trial shift the paradigm of ICU management away from routine deep sedation and paralysis, and how can attendings effectively champion a culture of light sedation and early mobility in severe ARDS?

Key Response

Focuses on practice-changing implications and team leadership, emphasizing the modern ICU paradigm of minimizing iatrogenic harm by avoiding deep sedation unless absolutely necessary for rescue maneuvers.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

The ROSE trial was stopped early for futility after an interim analysis. What are the methodological implications of early stopping for futility in a large randomized controlled trial, and how does this affect the precision of the effect size for future meta-analyses?

Key Response

Critiques statistical design. Early stopping reduces power and truncates the sample size, widening confidence intervals and potentially obscuring small but clinically significant subgroup effects, complicating future trial design and systematic reviews.

Journal Editor
Journal Editor

As a peer reviewer assessing the ROSE trial, how does the unblinded, pragmatic design introduce performance bias, specifically regarding co-interventions like fluid management and vasopressor use in the context of deep sedation?

Key Response

Examines threats to internal validity. Unblinded clinicians managing the deep sedation protocol in the intervention arm may have altered hemodynamic support compared to the lighter-sedated control arm, potentially confounding the mortality outcome with iatrogenic cardiovascular complications.

Guideline Committee
Guideline Committee

The 2017 ATS/ESICM guidelines previously issued a strong recommendation for early neuromuscular blockade in moderate-to-severe ARDS based on ACURASYS. Using GRADE methodology, how does the inclusion of the ROSE trial data justify downgrading this recommendation, and what should the new guidance state?

Key Response

Addresses guideline evolution. The ROSE trial introduced significant inconsistency in the evidence base and highlighted the harms of mandatory deep sedation, prompting a downgrade from a strong recommendation to a conditional recommendation against routine use, reserving NMB for specific rescue indications.

Clinical Landscape

Noteworthy Related Trials

2000

ARMA Trial

n = 861 · NEJM

Tested

Low tidal volume ventilation at 6 ml per kg

Population

Patients with acute lung injury and ARDS

Comparator

Traditional tidal volume ventilation at 12 ml per kg

Endpoint

Mortality before discharge home and ventilator-free days

Key result: Ventilation with lower tidal volumes resulted in decreased mortality and increased days without ventilator use.
2010

ACURASYS Trial

n = 340 · NEJM

Tested

Cisatracurium besylate for 48 hours

Population

Patients with severe ARDS

Comparator

Placebo

Endpoint

90-day in-hospital mortality

Key result: Early administration of cisatracurium improved 90-day survival and increased time off the ventilator without increasing ICU-acquired weakness.
2013

PROSEVA Trial

n = 466 · NEJM

Tested

Prone positioning for at least 16 hours per day

Population

Patients with severe ARDS

Comparator

Supine positioning

Endpoint

28-day all-cause mortality

Key result: Early application of prolonged prone positioning significantly decreased 28-day and 90-day mortality in patients with severe ARDS.

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