Lancet December 03, 2022

Safety, tolerability and efficacy of up-titration of guideline-directed medical therapies for acute heart failure (STRONG-HF): a multinational, open-label, randomised, trial

Alexandre Mebazaa, Beth Davison, Ovidiu Chioncel, Alain Cohen-Solal, Rafael Diaz, Gerasimos Filippatos, Marco Metra, Piotr Ponikowski, Karen Sliwa, Adriaan A Voors, et al.

Bottom Line

In patients recently hospitalized for acute heart failure, a high-intensity care strategy of rapid up-titration of guideline-directed medical therapies to target doses within two weeks of discharge safely and significantly reduced 180-day heart failure readmission or all-cause death.

Key Findings

1. The trial was terminated early by the data and safety monitoring board due to overwhelming efficacy in the high-intensity care intervention arm [2.5].
2. The primary composite endpoint of 180-day all-cause death or heart failure readmission occurred in 15.2% of the high-intensity care group versus 23.3% of the usual care group (absolute risk difference 8.1%; risk ratio 0.66, 95% CI 0.50-0.86; p=0.0021).
3. By day 90, patients in the high-intensity care group were vastly more likely to achieve 100% of target doses for renin-angiotensin blockers (55% vs 2%), beta-blockers (49% vs 4%), and mineralocorticoid receptor antagonists (84% vs 46%).
4. Overall adverse events by 90 days were more frequent in the high-intensity group (41% vs 29%), predominantly driven by hypotension and hyperkalemia.
5. Despite higher overall adverse events, the rates of serious adverse events (16% vs 17%) and fatal adverse events (5% vs 6%) were similar between the high-intensity and usual care groups.
6. Patients receiving high-intensity care experienced a significantly greater improvement in quality of life and physiological congestion markers (NT-proBNP, weight, blood pressure) by day 90 compared to usual care.

Study Design

Design
RCT
Open-Label
Sample
1,078
Patients
Duration
180 days
Median
Setting
Multinational
Population Patients aged 18 to 85 years admitted to the hospital with acute heart failure who were hemodynamically stable and not receiving full target doses of guideline-directed medical therapies.
Intervention High-intensity care involving initiation of half-target doses of guideline-directed medical therapies (renin-angiotensin blockers, beta-blockers, and MRAs) prior to discharge, with rapid up-titration to 100% of target doses within 2 weeks of discharge, accompanied by frequent outpatient visits and NT-proBNP monitoring.
Comparator Usual care, consisting of routine post-discharge follow-up according to local clinical practice, with no mandated rapid up-titration.
Outcome A composite of all-cause death or hospital readmission for heart failure at 180 days.

Study Limitations

The open-label design may have introduced investigator or patient bias, particularly regarding subjective measurements such as quality of life and adverse event reporting.
Sodium-glucose cotransporter-2 (SGLT2) inhibitors were not mandated in the titration protocol (prescribed to only ~10% of intervention patients), as the trial was designed before their broad integration into acute heart failure guidelines.
The high-intensity follow-up strategy, which required 4 clinical visits and routine laboratory/NT-proBNP monitoring within the first 6 weeks post-discharge, is highly resource-intensive and may present logistical challenges for widespread implementation in routine practice.
The trial was conducted partially during the COVID-19 pandemic, which may have influenced background all-cause mortality and threshold for hospital readmissions, although sensitivity analyses supported the robustness of the primary findings.

Clinical Significance

STRONG-HF provides robust randomized evidence to aggressively combat clinical inertia in the vulnerable post-discharge phase for heart failure patients. The findings unequivocally demonstrate that early, rapid up-titration of multiple guideline-directed medical therapies to target doses—rather than the traditional cautious, delayed, or sequential approach—is highly effective, safe, and saves lives, strongly supporting the systemic implementation of intensive transitional care clinics.

Historical Context

Historically, clinicians approached heart failure medication titration with caution, initiating drugs sequentially over many months to avoid theoretical adverse events like hypotension or renal dysfunction. This led to widespread 'clinical inertia'; registries repeatedly demonstrated that fewer than 5% of eligible heart failure patients ever reached optimal target doses of combination medical therapy following acute hospitalizations. Prior to STRONG-HF, landmark heart failure trials mostly evaluated single investigational agents in stable outpatient populations. STRONG-HF shifted the paradigm by evaluating a bundled treatment delivery strategy specifically targeting the high-risk, immediate post-discharge vulnerable period, validating a profound shift toward the simultaneous and rapid optimization of foundational medical therapy.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

What physiological mechanisms explain why rapid up-titration of the four pillars of guideline-directed medical therapy (GDMT) during the vulnerable post-discharge phase significantly reduces heart failure readmissions compared to delayed outpatient titration?

Key Response

Tests understanding of the vulnerable phase of acute heart failure, where early neurohormonal blockade (RAAS inhibition, sympathetic blockade) and natriuretic peptide enhancement rapidly reduce myocardial wall stress, prevent adverse remodeling, and stabilize fluid balance before a relapse occurs.

Resident
Resident

During the rapid up-titration protocol seen in STRONG-HF, patients frequently develop mild asymptomatic hypotension or mild serum creatinine elevations. How should a clinician differentiate between an expected physiological response to GDMT and an adverse event requiring dose reduction?

Key Response

Addresses a major practical challenge and clinical pitfall. Residents must learn that mild, asymptomatic drops in blood pressure and permissible bumps in creatinine (up to 30%) are expected hemodynamic responses to decongestion and RAAS/SGLT2 inhibition, and should not reflexively prompt the cessation of life-saving GDMT.

Fellow
Fellow

The STRONG-HF trial uniquely utilized early NT-proBNP levels (assessed at 1 week post-discharge) as a safety gatekeeper for further GDMT up-titration. What are the physiological limitations and potential confounders of relying on NT-proBNP to guide titration in complex sub-populations, such as those with severe CKD, obesity, or atrial fibrillation?

Key Response

Pushes fellows to critically analyze biomarker-guided therapy. While STRONG-HF required NT-proBNP to be less than 10% above discharge levels for safe titration, fellows must recognize that obesity falsely lowers these levels, while CKD and atrial fibrillation elevate them, necessitating a nuanced, individualized approach to biomarker interpretation rather than blind adherence to a trial protocol.

Attending
Attending

Implementing the STRONG-HF high-intensity protocol requires extensive outpatient resources, including clinical and laboratory follow-up at weeks 1, 2, 3, and 6. How can an attending physician lead the restructuring of heart failure transitional care clinics to make this resource-heavy approach feasible, effectively overcoming clinical inertia without overwhelming clinic capacity?

Key Response

Focuses on systems-based practice and overcoming structural barriers to care. Attendings must translate ideal trial protocols into real-world workflows, potentially leveraging pharmacist-led titration clinics, advanced practice providers, or remote patient monitoring to achieve the trial's rigorous follow-up cadence and combat the pervasive clinical inertia seen in standard practice.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

STRONG-HF was an open-label study that was terminated early for efficacy by the Data and Safety Monitoring Board after only 1078 of the planned 1800 patients were enrolled. How does the combination of an open-label design and an early stopping rule risk inflating the estimated treatment effect size, and what statistical or methodological safeguards could be employed to mitigate this overestimation?

Key Response

Explores the statistical concept of random high truncation. Trials stopped early for benefit often overestimate the true effect size due to regression to the mean. Combined with an open-label design, which introduces performance and ascertainment biases, PhD researchers must evaluate whether the dramatic effect size is entirely robust or partially an artifact of the trial design.

Journal Editor
Journal Editor

When assessing the validity of the STRONG-HF findings, a critical reviewer must heavily scrutinize the usual care arm. To what extent did the usual care arm reflect contemporary optimal medical management, and how can an editor determine if the observed benefit stems from the high-intensity strategy itself or merely from the prevention of profound clinical inertia that artificially disadvantaged the control group?

Key Response

Highlights the importance of the control arm in clinical trials. If the usual care group experienced widespread clinical inertia with exceptionally low rates of GDMT up-titration, the trial might simply prove that standard care is inadequate rather than proving a specific high-intensity timeline is superior to a well-managed standard timeline, a crucial distinction for editorial significance.

Guideline Committee
Guideline Committee

Current heart failure guidelines advocate for optimizing GDMT prior to and early after discharge, but lack strict timeline mandates. Based on the STRONG-HF data, should future guidelines elevate rapid up-titration (achieving 100% of target doses within 2 weeks of discharge) to a Class I recommendation, and how must the guidelines incorporate the intensive clinical and biomarker safety monitoring utilized in the trial to prevent real-world harm?

Key Response

Translates clinical trial data into formalized guidelines. The committee must weigh the strong outcome benefits against the feasibility and safety profile of rapid titration. If recommending this as a Class I or IIa intervention, guidelines must explicitly link the rapid titration to the mandatory frequent safety checks (labs, clinical volume status, NT-proBNP) to ensure the intervention remains safe when applied outside the controlled environment of a clinical trial.

Clinical Landscape

Noteworthy Related Trials

2019

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Comparator

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Endpoint

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2020

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Endpoint

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Key result: Sotagliflozin therapy initiated before or shortly after discharge significantly decreased cardiovascular deaths and heart failure events.
2022

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n = 530 · Nature Medicine

Tested

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Population

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Comparator

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Endpoint

Hierarchical composite of all-cause death, HF events, time to first HF event, and change in KCCQ-TSS

Key result: Patients treated with empagliflozin had a significantly greater likelihood of experiencing a clinical benefit compared to placebo at 90 days.

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