Journal of Clinical Oncology NOVEMBER 03, 2022

Durvalumab With or Without Tremelimumab in Combination With Chemotherapy as First-Line Therapy for Metastatic Non–Small-Cell Lung Cancer: The Phase III POSEIDON Study

Melissa L. Johnson, Byoung Chul Cho, Sarayut Lucien Geater, Maen Hussein, Luiz Henrique Araujo, Haruhiro Saito, et al.

Bottom Line

The POSEIDON trial demonstrated that a limited course of the anti-CTLA-4 antibody tremelimumab added to durvalumab and platinum-based chemotherapy significantly improved overall and progression-free survival compared to chemotherapy alone in first-line metastatic NSCLC.

Key Findings

1. The triplet regimen (tremelimumab, durvalumab, and chemotherapy) significantly improved overall survival (OS) compared to chemotherapy alone, with a median OS of 14.0 months versus 11.7 months (hazard ratio [HR] 0.77; 95% CI, 0.65–0.92; P=0.0030).
2. Progression-free survival (PFS) was also significantly improved with the triplet regimen versus chemotherapy alone, with a median PFS of 6.2 months versus 4.8 months (HR 0.72; 95% CI, 0.60–0.86; P=0.0003).
3. Treatment with durvalumab plus chemotherapy alone significantly improved PFS compared to chemotherapy alone (median 5.5 vs 4.8 months; HR 0.74; 95% CI, 0.62–0.89; P=0.0009), but the trend for improved OS did not reach statistical significance (median 13.3 vs 11.7 months; HR 0.86; 95% CI, 0.72–1.02; P=0.0758).
4. The triplet regimen maintained a manageable safety profile despite the addition of tremelimumab, with grade 3/4 treatment-related adverse events occurring in 51.8% of patients in the triplet arm compared to 44.4% in the chemotherapy arm.

Study Design

Design
RCT
Open-Label
Sample
1,013
Patients
Duration
34.9 mo
Median
Setting
Multicenter, global
Population Treatment-naive patients with EGFR/ALK wild-type metastatic non-small cell lung cancer
Intervention Tremelimumab 75 mg plus durvalumab 1,500 mg and platinum-based chemotherapy for 4 cycles, followed by durvalumab maintenance and one additional dose of tremelimumab at week 16
Comparator Platinum-based chemotherapy alone for up to 6 cycles (with or without maintenance pemetrexed)
Outcome Progression-free survival (PFS) and overall survival (OS)

Study Limitations

The study was open-label, which could introduce potential bias in reporting and patient management.
The study focused on a global population, but results might vary across specific regional clinical practices or health systems.
The exploratory analyses involving specific molecular subgroups (e.g., STK11, KEAP1, KRAS mutations) involve smaller sample sizes and should be interpreted as hypothesis-generating.
Comparative efficacy versus other standard-of-care immunotherapy-based regimens, such as pembrolizumab plus chemotherapy or nivolumab plus ipilimumab plus chemotherapy, was not directly evaluated.

Clinical Significance

The POSEIDON results establish a limited-duration anti-CTLA-4 plus anti-PD-L1 chemoimmunotherapy regimen as a viable first-line treatment option for metastatic NSCLC, specifically providing a durable benefit that extends to difficult-to-treat patient subgroups and those with low PD-L1 expression.

Historical Context

The POSEIDON trial builds upon the success of the PACIFIC trial (durvalumab in stage III NSCLC) and the CASPIAN trial (durvalumab in extensive-stage SCLC), exploring whether the addition of the CTLA-4 inhibitor tremelimumab could overcome resistance and provide deeper, more durable clinical responses in the first-line metastatic NSCLC setting.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

Explain the synergistic mechanism behind combining an anti-CTLA-4 agent like tremelimumab with an anti-PD-L1 agent like durvalumab in metastatic NSCLC.

Key Response

CTLA-4 inhibition (tremelimumab) acts primarily during the 'priming' phase of the immune response in the lymph nodes by increasing T-cell diversity and activation. PD-L1 inhibition (durvalumab) acts during the 'effector' phase within the tumor microenvironment to overcome T-cell exhaustion. Combining them targets two distinct phases of the cancer-immunity cycle, theoretically overcoming resistance mechanisms that occur when only one pathway is blocked.

Resident
Resident

Which specific patient subgroup in the POSEIDON trial appeared to derive a particularly meaningful benefit from the addition of tremelimumab to durvalumab and chemotherapy, especially when compared to historical outcomes?

Key Response

Post-hoc analyses of POSEIDON suggest that patients with STK11, KEAP1, and KRAS mutations—traditionally associated with poor prognosis and 'cold' tumors resistant to PD-(L)1 monotherapy—showed improved outcomes with the triplet (D+T+C) regimen. This makes the POSEIDON regimen a strong clinical consideration for patients with these specific genomic alterations where chemotherapy or PD-L1 inhibitors alone often fail.

Fellow
Fellow

Contrast the 'limited course' tremelimumab strategy used in POSEIDON with the dosing schedule of ipilimumab in the CheckMate 9LA trial. How might these differences impact long-term immune-related adverse events (irAEs)?

Key Response

POSEIDON utilized only 5 doses of tremelimumab (a limited course over 16 weeks), whereas CheckMate 9LA utilized ipilimumab every 6 weeks until progression or toxicity. The POSEIDON approach aims to provide the necessary 'priming' stimulus while limiting the cumulative toxicity and late-onset irAEs typically associated with prolonged CTLA-4 blockade, potentially improving the long-term tolerability of the triplet combination.

Attending
Attending

The POSEIDON trial showed a statistically significant OS benefit for D+T+C over chemotherapy, but the D+C arm did not reach statistical significance for OS. How does this finding influence your decision to use 'dual' vs 'single' checkpoint inhibition in the first-line setting?

Key Response

The failure of the D+C arm to reach OS significance despite a PFS benefit suggests that for many patients, PD-L1 inhibition plus chemotherapy is insufficient to change the natural history of the disease. The OS benefit in the D+T+C arm reinforces the concept that CTLA-4 inhibition provides a survival 'tail' that PD-L1 inhibition alone may not, particularly in PD-L1 low or negative expressors, shifting the practice toward triplets for high-risk clinical phenotypes.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

Critique the statistical hierarchy and alpha-spending strategy employed in POSEIDON regarding the dual primary endpoints of PFS and OS. How did the testing sequence affect the interpretability of the D+C arm results?

Key Response

POSEIDON used a complex gatekeeping strategy to control the family-wise error rate across multiple comparisons. Because the alpha was split between PFS and OS and across two experimental arms (D+T+C and D+C), the D+C arm required a very stringent p-value to claim OS significance. Even though D+C showed a numeric improvement, it failed to meet the pre-specified threshold, highlighting the 'statistical penalty' inherent in multi-arm trials with multiple primary endpoints.

Journal Editor
Journal Editor

Considering the current standard of care established by KEYNOTE-189, how does the control arm of platinum-based chemotherapy in POSEIDON limit the study's internal and external validity for a 2024 editorial perspective?

Key Response

When POSEIDON began, chemotherapy was a standard control. However, by the time of publication, chemo-immunotherapy (e.g., Pembrolizumab/Chemo) became the global standard. A 'tough' reviewer would flag that POSEIDON lacks a direct head-to-head comparison with the current standard of care (PD-1 + Chemo), making it difficult to definitively conclude if D+T+C is superior to the regimens most clinicians are currently using.

Guideline Committee
Guideline Committee

Based on the POSEIDON data, should guideline bodies (like NCCN or ESMO) elevate the D+T+C regimen to a 'Preferred' status for all metastatic NSCLC, or should it be restricted to specific PD-L1 strata?

Key Response

Current NCCN guidelines (v2.2024) list D+T+C as a Category 1 recommendation for first-line NSCLC. However, the most robust OS benefit was observed in the PD-L1 <1% and 1-49% groups. Given the toxicity profile of CTLA-4 inhibitors, committees may prioritize it for PD-L1 <1% (similar to CheckMate 9LA) or for patients with STK11/KEAP1 mutations, rather than replacing Pembrolizumab+Chemo for PD-L1 >50% patients where single-agent PD-1 is often sufficient.

Clinical Landscape

Noteworthy Related Trials

2018

KEYNOTE-189 Trial

n = 616 · NEJM

Tested

Pembrolizumab plus pemetrexed and platinum-based chemotherapy

Population

Patients with previously untreated metastatic non-squamous NSCLC without EGFR or ALK mutations

Comparator

Placebo plus pemetrexed and platinum-based chemotherapy

Endpoint

Overall survival and progression-free survival

Key result: The addition of pembrolizumab to chemotherapy resulted in significantly longer overall survival and progression-free survival compared to chemotherapy alone.
2019

MYSTIC Trial

n = 1118 · Lancet Oncol

Tested

Durvalumab plus tremelimumab or durvalumab monotherapy

Population

Treatment-naive patients with stage IV NSCLC

Comparator

Platinum-based chemotherapy

Endpoint

Overall survival and progression-free survival in patients with high PD-L1 expression

Key result: The combination of durvalumab and tremelimumab did not significantly improve overall survival compared to platinum-based chemotherapy in the first-line setting.
2020

CheckMate 9LA Trial

n = 719 · Lancet Oncol

Tested

Nivolumab plus ipilimumab combined with limited-duration platinum-doublet chemotherapy

Population

Patients with metastatic NSCLC regardless of PD-L1 expression

Comparator

Platinum-doublet chemotherapy alone

Endpoint

Overall survival

Key result: The combination of nivolumab and ipilimumab with short-course chemotherapy demonstrated superior overall survival compared to chemotherapy alone.

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