The New England Journal of Medicine OCTOBER 28, 2024

Transcatheter Aortic-Valve Replacement for Asymptomatic Severe Aortic Stenosis

Philippe Généreux, Allan Schwartz, J. Bradley Oldemeyer, et al. for the EARLY TAVR Trial Investigators

Bottom Line

In patients with asymptomatic severe aortic stenosis, early intervention with transcatheter aortic-valve replacement (TAVR) significantly reduced the composite risk of death, stroke, or unplanned cardiovascular hospitalization compared to clinical surveillance over a median follow-up of 3.8 years.

Key Findings

1. The primary endpoint (composite of all-cause death, stroke, or unplanned cardiovascular hospitalization) occurred in 26.8% of the early TAVR group compared to 45.3% in the clinical surveillance group (hazard ratio, 0.50; 95% CI, 0.40 to 0.63; P<0.001).
2. The benefit was largely driven by a substantial reduction in unplanned cardiovascular hospitalizations (20.9% in the TAVR group vs. 41.7% in the surveillance group).
3. Clinical surveillance patients experienced a high rate of delayed valve replacement, with 87% undergoing the procedure during follow-up, often necessitated by the onset of acute symptoms.
4. Early TAVR demonstrated an excellent safety profile, with procedure-related adverse event rates similar to those seen in the deferred intervention cohort.

Study Design

Design
RCT
Open-Label
Sample
901
Patients
Duration
3.8 yr
Median
Setting
Multicenter, US/Canada
Population Patients aged 65 years and older with asymptomatic severe aortic stenosis and preserved left ventricular ejection fraction
Intervention Early transfemoral transcatheter aortic-valve replacement (TAVR)
Comparator Clinical surveillance with delayed intervention upon onset of symptoms
Outcome Composite of all-cause death, stroke, or unplanned hospitalization for cardiovascular causes

Study Limitations

The trial was open-label, which may have introduced biases in clinical decision-making or patient reporting regarding symptoms and hospitalizations.
The study did not include a surgical aortic valve replacement (SAVR) arm, limiting comparisons to transcatheter approaches.
The findings may not be generalizable to all patient populations, such as those with complex bicuspid valve anatomy or very high surgical risk, who were largely excluded.
The unanticipated disparity in stroke rates between groups requires further investigation to determine if it reflects a true treatment effect or other factors.

Clinical Significance

These results challenge the long-standing 'watchful waiting' paradigm for asymptomatic severe aortic stenosis, suggesting that proactive intervention with TAVR may prevent the unpredictable decline and adverse clinical events associated with the onset of symptoms.

Historical Context

For over 60 years, clinical guidelines have favored conservative management and delayed intervention for asymptomatic severe aortic stenosis until symptoms manifest. The EARLY TAVR trial serves as the first major randomized controlled trial to directly test the safety and efficacy of early prophylactic TAVR in this population, potentially reshaping future standard-of-care recommendations.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

What is the physiological rationale for performing a treadmill stress test in a patient who claims to be asymptomatic with severe aortic stenosis, and how does the EARLY-TAVR study challenge the traditional 'watchful waiting' approach?

Key Response

Historically, surgery was deferred until symptom onset because the risks of surgery outweighed the low risk of sudden death in truly asymptomatic patients. However, many patients are 'pseudo-asymptomatic' due to sedentary lifestyles. The stress test unmasks symptoms or abnormal BP responses. EARLY-TAVR suggests that even in those who appear asymptomatic, early intervention with a lower-risk TAVR procedure prevents the cumulative risk of unplanned hospitalizations and cardiac damage that occurs during the surveillance period.

Resident
Resident

A 75-year-old patient with an aortic valve area of 0.7 cm² and a mean gradient of 45 mmHg denies any chest pain or dyspnea. According to the EARLY-TAVR trial results, what is the primary benefit of intervening now versus waiting for the patient to report symptoms?

Key Response

The trial demonstrated that early TAVR significantly reduced the composite endpoint of death, stroke, or unplanned cardiovascular hospitalization (hazard ratio 0.50). The benefit was largely driven by a reduction in unplanned hospitalizations (over 20% absolute risk reduction). This shifts management from reacting to clinical decompensation to proactive prevention of adverse events.

Fellow
Fellow

The EARLY-TAVR trial included a high-gradient population (mean gradient ≥40 mmHg or Vmax ≥4.0 m/s). How should these findings be integrated with the results of the RECOVERY and AVATAR trials, and do they apply to patients with low-flow, low-gradient asymptomatic stenosis?

Key Response

RECOVERY and AVATAR both showed mortality benefits for early SAVR in asymptomatic severe AS, but EARLY-TAVR is the first large-scale trial to prove the benefit of a transcatheter approach. However, EARLY-TAVR specifically enrolled patients with high-gradient AS and preserved EF. Patients with low-gradient AS (even with low EF) were not the focus here, so the findings cannot be directly extrapolated to the low-gradient population without further data.

Attending
Attending

In the context of 'shared decision-making,' how does the 3.8-year median follow-up of EARLY-TAVR influence your discussion with a 65-year-old asymptomatic patient regarding valve durability versus the immediate benefits of early intervention?

Key Response

While EARLY-TAVR shows clear mid-term benefits in reducing hospitalizations and composite events, the 3.8-year follow-up is relatively short for a younger patient. The 'attending level' insight is balancing the prevention of mid-term morbidity against the long-term uncertainty of TAVR durability and the potential need for future 'TAVR-in-TAVR' or high-risk explant later in life, which was not the primary focus of this study.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

Evaluate the impact of the 40% crossover rate from the surveillance arm to TAVR on the study's power and the interpretation of the intention-to-treat (ITT) analysis. Does this crossover rate suggest a 'failure' of the surveillance strategy or a limitation of the trial's ability to show a mortality benefit?

Key Response

The high crossover rate is expected in a trial where the control arm is surveillance for a progressive disease. While ITT maintains randomization integrity, the rapid transition to TAVR once symptoms appeared in the surveillance group likely diluted the potential mortality difference between the two arms. This suggests that 'clinical surveillance' in practice often leads to intervention anyway, but 'early' intervention simply captures the benefit of preventing the first unplanned event.

Journal Editor
Journal Editor

As a reviewer, how would you address the lack of blinding and the use of 'unplanned cardiovascular hospitalization' as a major driver of the composite primary endpoint in EARLY-TAVR?

Key Response

Unblinded trials are susceptible to ascertainment bias, particularly for 'softer' endpoints like hospitalization. A clinician who knows a patient has untreated severe AS may be more likely to admit them for minor cardiac symptoms than a patient who has already undergone TAVR. A rigorous review would demand a strict, blinded adjudication committee for all hospitalizations to ensure they met objective criteria for 'unplanned' and 'cardiovascular' to mitigate this bias.

Guideline Committee
Guideline Committee

The 2020 ACC/AHA guidelines currently give a Class 1 recommendation for intervention in asymptomatic AS only if LVEF <50% or if symptoms are unmasked by exercise testing. Does EARLY-TAVR provide sufficient evidence to move the recommendation for asymptomatic high-gradient AS with preserved EF to Class 1?

Key Response

EARLY-TAVR provides high-quality (Level A) evidence that early TAVR is superior to surveillance. Combined with RECOVERY and AVATAR (SAVR trials), there is now a consistent body of evidence across both surgical and transcatheter modalities. The committee must decide if the reduction in hospitalizations and the clear safety of TAVR justify a Class 1 (Benefit >>> Risk) recommendation for all high-gradient asymptomatic patients, potentially removing the requirement for a stress test.

Clinical Landscape

Noteworthy Related Trials

2010

PARTNER 1 Trial

n = 699 · NEJM

Tested

Transcatheter aortic-valve replacement (TAVR)

Population

Patients with severe aortic stenosis at high risk for surgery

Comparator

Surgical aortic-valve replacement (SAVR)

Endpoint

All-cause mortality at 1 year

Key result: TAVR was non-inferior to surgical valve replacement in high-risk patients, establishing TAVR as a viable alternative.
2010

RECOVERY Trial

n = 145 · Circulation

Tested

Early surgical aortic-valve replacement

Population

Asymptomatic patients with very severe aortic stenosis

Comparator

Conservative management (watchful waiting)

Endpoint

Operative mortality or cardiovascular death

Key result: Early surgery was associated with significantly lower operative and cardiovascular mortality compared to conservative management.
2019

PARTNER 3 Trial

n = 1000 · NEJM

Tested

Transcatheter aortic-valve replacement (TAVR)

Population

Patients with severe aortic stenosis at low surgical risk

Comparator

Surgical aortic-valve replacement (SAVR)

Endpoint

Composite of death, stroke, or rehospitalization at 1 year

Key result: TAVR resulted in a significantly lower rate of the primary composite endpoint compared to surgery in low-risk patients.

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