JAMA JANUARY 01, 2019

Effect of Linagliptin vs Placebo on Major Cardiovascular Events in Adults With Type 2 Diabetes and High Cardiovascular and Renal Risk: The CARMELINA Randomized Clinical Trial

Julio Rosenstock, Vlado Perkovic, Odd Erik Johansen, Mark E. Cooper, Steven E. Kahn, Nikolaus Marx, John H. Alexander, et al.

Bottom Line

The CARMELINA trial demonstrated that adding linagliptin to standard care in adults with type 2 diabetes and high cardiovascular and renal risk is cardiovascularly safe and does not increase the risk of hospitalization for heart failure or renal progression compared to placebo.

Key Findings

1. Linagliptin was non-inferior to placebo for the primary composite endpoint of cardiovascular death, nonfatal myocardial infarction, or nonfatal stroke (12.4% in the linagliptin group vs 12.1% in the placebo group; HR, 1.02; 95% CI, 0.89-1.17).
2. There was no significant difference in the risk of hospitalization for heart failure between treatment groups (6.0% in the linagliptin group vs 6.5% in the placebo group; HR, 0.90; 95% CI, 0.74-1.08).
3. Renal outcomes, defined as end-stage kidney disease, sustained decrease in eGFR of 40% or more, or renal death, occurred in 9.4% of the linagliptin group and 8.8% of the placebo group (HR, 1.04; 95% CI, 0.89-1.22), indicating no significant risk increase.
4. The use of linagliptin was associated with a modest but statistically significant reduction in HbA1c (difference of 0.36%) compared to placebo over the duration of the trial.

Study Design

Design
RCT
Double-Blind
Sample
6,979
Patients
Duration
2.2 yr
Median
Setting
Multicenter, 27 countries
Population Adults with type 2 diabetes, HbA1c 6.5%-10.0%, and high cardiovascular and/or renal risk (defined by established vascular disease and/or impaired kidney function).
Intervention Linagliptin 5 mg once daily plus standard care.
Comparator Matching placebo once daily plus standard care.
Outcome Time to first occurrence of cardiovascular death, nonfatal myocardial infarction, or nonfatal stroke (3-point MACE).

Study Limitations

The study was specifically powered for cardiovascular non-inferiority, which may limit the ability to detect subtle differences in efficacy for specific sub-outcomes.
Patients with severe end-stage renal disease were excluded from the study, limiting the generalizability of results to this highest-risk population.
The median follow-up of 2.2 years may be insufficient to observe the full long-term effects of DPP-4 inhibition on chronic microvascular renal outcomes.
The trial was conducted against a background of standard care that included varying use of other glucose-lowering therapies, which might influence outcomes.

Clinical Significance

The trial confirms the cardiovascular safety profile of linagliptin in a high-risk population of patients with type 2 diabetes and comorbid cardiovascular or renal disease, providing clinicians confidence in its use without exacerbating heart failure or renal risk.

Historical Context

Following regulatory requirements for cardiovascular outcome trials (CVOTs) for all new glucose-lowering agents, CARMELINA was designed to assess the safety of linagliptin. It specifically targeted a high-risk population with established cardiorenal disease, a group often underrepresented in earlier diabetes trials, to address concerns about the class effect of DPP-4 inhibitors on heart failure and kidney safety.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

What is the mechanism of action of linagliptin, and what unique pharmacokinetic property makes it particularly relevant for the high-risk renal population studied in the CARMELINA trial?

Key Response

Linagliptin is a DPP-4 inhibitor that prevents the breakdown of incretin hormones like GLP-1 and GIP. Unlike other DPP-4 inhibitors (such as sitagliptin or saxagliptin), linagliptin is primarily excreted via the enterohepatic system (bile and feces) rather than the kidneys. This eliminates the need for dose adjustment across all stages of chronic kidney disease (CKD), which was a central focus of the CARMELINA trial's safety assessment.

Resident
Resident

The SAVOR-TIMI 53 trial with saxagliptin raised concerns about a potential class-wide risk of hospitalization for heart failure (hHF) with DPP-4 inhibitors. How do the CARMELINA results influence your clinical decision-making when selecting a glucose-lowering agent for a patient with T2DM and high cardiovascular risk?

Key Response

CARMELINA provided critical evidence that linagliptin is safe regarding heart failure, showing no increase in hHF (HR 0.90) compared to placebo. This differentiates it from saxagliptin and alogliptin. For residents, this means linagliptin can be used safely in patients with established cardiovascular disease or CKD without the specific heart failure concerns that plague other agents in the same class, though it remains secondary to SGLT2 inhibitors or GLP-1RAs if heart failure or renal protection is the primary goal.

Fellow
Fellow

While CARMELINA demonstrated cardiovascular safety (non-inferiority), it did not show a 'superiority' benefit for renal outcomes despite preclinical data suggesting anti-fibrotic effects of DPP-4 inhibition. How should a subspecialist reconcile these findings with the 'superiority' renal results seen in SGLT2 inhibitor trials like CREDENCE or DAPA-CKD?

Key Response

CARMELINA was designed primarily as a safety (non-inferiority) trial in a population with very advanced CKD (including eGFR down to 15). The neutrality of the composite renal endpoint (sustained ESRD, 40% GFR decline, or renal death) suggests that while linagliptin is safe, it lacks the potent hemodynamically-mediated and metabolic-protective effects of SGLT2 inhibitors. For a fellow, this highlights that linagliptin’s role in CKD is 'renal-neutral' glucose management rather than active 'renoprotection' or slowing disease progression.

Attending
Attending

In the context of 'value-based care,' how does the CARMELINA trial support the role of linagliptin for elderly patients with multi-morbidity and varying levels of renal function compared to more modern 'disease-modifying' therapies?

Key Response

Linagliptin offers a 'simplification' strategy. CARMELINA's inclusion of patients with high CV risk and advanced CKD (often excluded from other trials) proves that linagliptin is a safe 'set-and-forget' drug. It does not require GFR monitoring for dosing, has low hypoglycemia risk, and is weight-neutral. For an attending, this trial justifies linagliptin as a preferred agent for frail patients where the priority is avoiding harm (hypoglycemia, volume depletion, or heart failure exacerbation) while maintaining glycemic targets.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

CARMELINA utilized a non-inferiority margin of 1.3 for the upper bound of the 95% confidence interval for the primary MACE endpoint. Critique the choice of this margin and the implications of the high baseline CV event rate in this cohort for the statistical power of the trial.

Key Response

The 1.3 margin was the standard FDA requirement for CVOTs post-2008. Given that CARMELINA's population had extremely high risk (high CKD prevalence), the trial was well-powered to achieve a narrow confidence interval (0.81 to 1.14), which strongly supported safety. However, because the trial was driven by safety events, the PhD-level critique would focus on whether the 'neutral' renal findings were a result of the trial being underpowered for superiority or if the follow-up duration (median 2.2 years) was insufficient to see a divergence in renal outcomes in a population already at advanced stages of decline.

Journal Editor
Journal Editor

As a reviewer, what concerns would you raise regarding the generalizability of CARMELINA’s findings, specifically the 'neutral' heart failure signal, given the high prevalence of baseline heart failure in the study cohort compared to earlier DPP-4 inhibitor trials?

Key Response

An editor would flag that CARMELINA’s population was specifically enriched for high CV and renal risk, yet it showed an HR of 0.90 for hHF (numerically favoring linagliptin). This 'robustness' against the saxagliptin signal is a key editorial point. However, a reviewer would also ask if the frequent use of other background therapies (like ACE inhibitors or beta-blockers) in 2019 clinical practice could have masked potential signals or if the trial's design successfully mitigated the 'detection bias' for heart failure seen in earlier studies.

Guideline Committee
Guideline Committee

How does CARMELINA specifically address the gaps in the ADA/EASD consensus reports regarding the use of DPP-4 inhibitors in patients with an eGFR below 30 mL/min/1.73m², and should the 'heart failure' warning be removed from the class as a whole?

Key Response

The ADA/EASD guidelines emphasize SGLT2i and GLP-1RAs for high-risk patients. CARMELINA provides the highest level of evidence (Level 1A) for linagliptin's safety in the GFR <30 group, where SGLT2i options were previously limited. Regarding the class warning, CARMELINA (along with TECOS) suggests the heart failure risk is NOT a class effect. Therefore, guidelines should distinguish between 'safe' DPP-4s (linagliptin, sitagliptin) and those with a 'caution' or 'contraindication' in heart failure (saxagliptin, alogliptin).

Clinical Landscape

Noteworthy Related Trials

2013

SAVOR-TIMI 53 Trial

n = 16,492 · NEJM

Tested

Saxagliptin

Population

T2DM patients with history of or risk factors for CV disease

Comparator

Placebo

Endpoint

3-point MACE

Key result: Saxagliptin did not increase or decrease the rate of ischemic events, but was associated with an increased rate of hospitalization for heart failure.
2015

EMPA-REG OUTCOME Trial

n = 7,020 · NEJM

Tested

Empagliflozin

Population

T2DM patients with high CV risk

Comparator

Placebo

Endpoint

3-point MACE

Key result: Empagliflozin significantly reduced the risk of cardiovascular death compared to placebo.
2015

TECOS Trial

n = 14,671 · NEJM

Tested

Sitagliptin

Population

T2DM patients with established cardiovascular disease

Comparator

Placebo

Endpoint

4-point MACE

Key result: Sitagliptin added to standard care did not increase the risk of major adverse cardiovascular events or hospitalization for heart failure.

Tailored to your role

Want this tailored to you?

Add your specialty or training stage to get role-specific takeaways and more questions.

Personalize this analysis