Annals of Hematology FEBRUARY 04, 2026

EPCORE NHL-1: Three-Year Follow-up of Subcutaneous Epcoritamab in Relapsed/Refractory Large B-Cell Lymphoma

Karimi Y, Vose J, Clausen MR, et al.

Bottom Line

The phase I/II EPCORE NHL-1 trial demonstrates that epcoritamab induces durable, long-term responses in heavily pretreated patients with relapsed/refractory large B-cell lymphoma, with median progression-free survival and overall survival outcomes supporting its therapeutic potential in this high-risk population.

Key Findings

1. At a median follow-up of 37.1 months, the overall response rate (ORR) was 59% (95% CI, 50.5–66.4), with 41% of patients achieving a complete response (CR).
2. Responses were durable, with a median duration of response (DoR) of 20.8 months (95% CI, 13.0–32.0) and a median duration of CR of 36.1 months.
3. Patients who achieved a CR experienced favorable long-term outcomes, with a 3-year progression-free survival (PFS) estimate of 52% and an overall survival (OS) median not reached.
4. Assessment of minimal residual disease (MRD) in 119 evaluable patients showed 45% achieved MRD negativity at some point, which significantly correlated with superior outcomes (3-year PFS of 52% in MRD-negative vs 18% in MRD-positive patients).
5. The long-term safety profile remained consistent with initial reports, with no new emergence of severe cytokine release syndrome (CRS) or immune effector cell-associated neurotoxicity syndrome (ICANS) events.

Study Design

Design
Phase I/II Clinical Trial
Open-Label
Sample
157
Patients
Duration
37.1 mo
Median
Setting
Multicenter, Global
Population Adults with relapsed/refractory CD20+ mature B-cell non-Hodgkin lymphoma (including DLBCL, high-grade B-cell lymphoma, and follicular lymphoma) who received ≥2 prior lines of systemic therapy.
Intervention Subcutaneous epcoritamab (0.16 mg and 0.8 mg step-up doses, followed by 48-mg full doses) administered in 28-day cycles.
Comparator N/A
Outcome Overall response rate (ORR) per Lugano criteria

Study Limitations

The study is a non-randomized, single-arm, open-label trial, which inherently lacks a direct concurrent comparator group to quantify comparative efficacy against standard-of-care options.
The patient population was heterogeneous, including various B-cell lymphoma subtypes, and included heavily pretreated patients, potentially complicating generalizability to broader clinical practice.
MRD data was not available for the entire cohort, limiting the scope of biomarker-driven response analysis.
As an accelerated approval study, long-term clinical benefit is still subject to ongoing verification in larger confirmatory trials.

Clinical Significance

Epcoritamab provides a fixed-duration-like, 'off-the-shelf' immunotherapy alternative for patients with relapsed/refractory DLBCL who have failed multiple prior lines of therapy, including CAR T-cell therapy. Its subcutaneous administration profile and manageable toxicity suggest potential for outpatient delivery, significantly increasing accessibility compared to cell-based therapies.

Historical Context

The development of T-cell-engaging bispecific antibodies like epcoritamab represents a major evolution in immunotherapy following the success of CD19-targeting CAR T-cell therapies. By bridging CD3 on T-cells to CD20 on malignant B-cells, these agents bypass the manufacturing time and logistics required for autologous cellular products, addressing a critical gap for patients with aggressive, refractory disease.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

How does the 'bispecific' mechanism of epcoritamab facilitate T-cell mediated destruction of lymphoma cells, and why is this considered an improvement over traditional monoclonal antibodies like rituximab?

Key Response

Epcoritamab is a bispecific antibody that binds simultaneously to CD3 on T-cells and CD20 on B-cells (lymphoma). Unlike rituximab, which relies on the patient's innate immune system (complement and NK cells) for antibody-dependent cellular cytotoxicity, epcoritamab forces a physical synapse between cytotoxic T-cells and the cancer cell, triggering direct granzyme/perforin-mediated cell death regardless of the patient's existing immune 'fitness' or MHC expression.

Resident
Resident

In a patient receiving epcoritamab for R/R LBCL who develops fever and hypotension six hours after the first full dose, what are the immediate management priorities and how does the subcutaneous route of administration affect the typical onset of Cytokine Release Syndrome (CRS)?

Key Response

Management priorities include grading the CRS, starting aggressive fluid resuscitation, and administering tocilizumab (IL-6 receptor antagonist) if symptoms persist or escalate. Subcutaneous administration of epcoritamab generally results in a delayed T-max (peak concentration) of cytokines compared to IV bispecifics, meaning CRS may occur later (median onset ~2 days) but can still be life-threatening, necessitating vigilant monitoring during the 'step-up' dosing phase.

Fellow
Fellow

The EPCORE NHL-1 trial included a significant proportion of patients who progressed after CAR T-cell therapy. What does the 3-year follow-up suggest about the 'fitness' of the T-cell compartment in these patients, and does prior CAR T-cell exposure significantly diminish the durability of response to epcoritamab?

Key Response

The 3-year data indicates that epcoritamab can induce durable complete remissions even in the post-CAR T setting, suggesting that the endogenous T-cell pool remains functional enough to be redirected. While initial response rates may be slightly lower in post-CAR T patients compared to CAR T-naive patients, the 'tail of the curve' suggests that once a complete response is achieved, the durability is comparable, making it a viable salvage strategy for CAR T failures.

Attending
Attending

With the 3-year follow-up demonstrating a plateau in the duration of response for patients achieving a Complete Response (CR), should epcoritamab be viewed as a definitive curative therapy or primarily as a 'bridge' to allogeneic stem cell transplantation in the third-line setting?

Key Response

The EPCORE NHL-1 data shows a significant subset of CR patients remaining in remission at 3 years without subsequent transplant. This suggests that for patients achieving a deep molecular response, epcoritamab may be curative as a standalone agent. For the attending, this shifts the discussion from 'how do we get this patient to transplant?' to 'can we safely observe this patient?', especially in those who are transplant-ineligible due to age or comorbidities.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

Given that EPCORE NHL-1 was a single-arm expansion cohort, what are the primary statistical limitations in interpreting the 'long-term' Overall Survival (OS) benefit, and how should future trials utilize Minimal Residual Disease (MRD) kinetics to validate these findings?

Key Response

Single-arm trials suffer from selection bias and the lack of a contemporaneous control, making OS data difficult to contextualize against the rapidly evolving standard of care. PhD-level analysis should focus on the use of circulating tumor DNA (ctDNA) as a surrogate for MRD; demonstrating 'molecular clearance' at early time points could provide a more objective, mechanistic validation of the long-term durability seen in the clinical data, potentially serving as a predictive biomarker for treatment cessation.

Journal Editor
Journal Editor

A major concern in long-term follow-up of T-cell engaging therapies is 'immune exhaustion' and late-onset infectious complications. How does the EPCORE NHL-1 data address the trade-off between sustained lymphoma control and the cumulative risk of Grade 3+ infections over a 3-year period?

Key Response

As an editor, the focus is on the safety-efficacy balance. The paper must be scrutinized for whether the 'plateau' in efficacy is offset by a rising cumulative incidence of opportunistic infections or secondary malignancies. If the 3-year data shows that the rate of new Grade 3 infections decreases over time for those in continuous remission, it supports the feasibility of long-term bispecific therapy; conversely, persistent lymphopenia and hypogammaglobulinemia remain significant 'red flags' for long-term utility.

Guideline Committee
Guideline Committee

How do the 3-year EPCORE NHL-1 results influence the current NCCN/ESMO hierarchy for R/R LBCL, specifically regarding the choice between epcoritamab and other bispecifics like glofitamab or polatuzumab-based regimens in the third-line?

Key Response

Current guidelines (e.g., NCCN Category 2A) list epcoritamab as a preferred third-line option. The 3-year durability data provides a higher level of evidence (moving toward Category 1) and may favor epcoritamab over polatuzumab-BR, which typically lacks the same plateau of durability. The committee must decide if the subcutaneous convenience and long-term remission data are sufficient to recommend epcoritamab over glofitamab (which has a fixed-duration schedule) in patients where treatment-free intervals are a priority.

Clinical Landscape

Noteworthy Related Trials

2017

ZUMA-1 Trial

n = 101 · NEJM

Tested

Axicabtagene ciloleucel (CAR-T therapy)

Population

Relapsed/refractory large B-cell lymphoma

Comparator

Historical control

Endpoint

Objective response rate

Key result: CAR-T therapy produced durable responses in patients with chemorefractory large B-cell lymphoma who had limited treatment options.
2022

POLARIX Trial

n = 879 · NEJM

Tested

Polatuzumab vedotin + R-CHP

Population

Previously untreated diffuse large B-cell lymphoma

Comparator

R-CHOP

Endpoint

Investigator-assessed progression-free survival

Key result: The study demonstrated superior progression-free survival with the polatuzumab vedotin regimen compared to standard R-CHOP in previously untreated patients.
2022

Glofitamab NP30179 Trial

n = 155 · NEJM

Tested

Glofitamab

Population

Relapsed/refractory large B-cell lymphoma

Comparator

None (Single arm)

Endpoint

Complete response rate

Key result: Fixed-duration glofitamab induced high rates of complete response in patients with heavily pretreated large B-cell lymphoma.

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