The Lancet Child & Adolescent Health FEBRUARY 01, 2018

Maternal sildenafil for severe fetal growth restriction (STRIDER): a multicentre, randomised, placebo-controlled, double-blind trial

Zarko Alfirevic, et al.

Bottom Line

In this randomized, double-blind, placebo-controlled trial, sildenafil (25 mg three times daily) failed to prolong pregnancy or improve perinatal outcomes in women with severe early-onset fetal growth restriction.

Key Findings

1. The primary outcome of time from randomization to delivery showed no significant difference between groups, with a median of 17 days (IQR 7-24) in the sildenafil group versus 18 days (IQR 8-28) in the placebo group (p=0.23).
2. There was no significant difference in live births, with a relative risk (RR) of 1.06 (95% CI 0.84 to 1.33; p=0.62).
3. Neonatal outcomes, including fetal deaths (RR 0.89, 95% CI 0.54 to 1.45) and neonatal deaths (RR 1.33, 95% CI 0.54 to 3.28), did not differ significantly between the treatment and placebo arms.
4. Mean birthweight showed no significant improvement with sildenafil, with a difference of -14 g (95% CI -100 to 126; p=0.81) compared to placebo.

Study Design

Design
RCT
Double-Blind
Sample
135
Patients
Duration
Until delivery
Median
Setting
Multicentre, UK
Population Women with singleton pregnancies (22+0 to 29+6 weeks) diagnosed with severe early-onset fetal growth restriction, defined as estimated fetal weight or abdominal circumference below the 10th percentile and absent/reversed end-diastolic flow in the umbilical artery.
Intervention Oral sildenafil 25 mg three times daily until 32 weeks gestation or delivery.
Comparator Matching placebo three times daily until 32 weeks gestation or delivery.
Outcome Time from randomization to delivery, measured in days.

Study Limitations

The study was limited by a relatively small sample size, which may have impacted the power to detect smaller differences in secondary outcomes.
The trial was conducted in a specific, high-risk population of early-onset FGR, limiting the generalizability of findings to later-onset or less severe forms of the condition.
Potential risks, such as neonatal pulmonary hypertension, which were observed in other related STRIDER consortium trials, necessitate caution regarding the therapeutic profile of sildenafil for this indication.

Clinical Significance

The trial results indicate that sildenafil does not provide clinical benefit in managing severe early-onset fetal growth restriction. The investigators concluded that sildenafil should not be prescribed for this condition outside of controlled research settings.

Historical Context

The STRIDER (Sildenafil TheRapy In Dismal prognosis Early-onset fetal growth Restriction) collaboration was established to evaluate whether the vasodilator properties of the phosphodiesterase type 5 inhibitor sildenafil could improve uteroplacental perfusion. Despite promising results in early small-scale studies and animal models, the international consortium trials ultimately failed to demonstrate efficacy and, in some international arms, raised concerns regarding neonatal safety.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

Sildenafil is a phosphodiesterase type 5 (PDE5) inhibitor. What is the physiological mechanism by which this class of drug was hypothesized to improve fetal growth in cases of severe placental insufficiency?

Key Response

Sildenafil prevents the breakdown of cyclic guanosine monophosphate (cGMP), which enhances the vasodilatory effects of nitric oxide. In the context of fetal growth restriction (FGR), it was hypothesized that sildenafil would decrease uterine artery resistance and increase blood flow to the placenta (the 'placental bed'), thereby improving the delivery of oxygen and nutrients to the fetus.

Resident
Resident

In the management of a pregnancy complicated by severe early-onset FGR (<27 weeks), how should the findings of the STRIDER trial influence your response to a patient asking about experimental medications to 'help the baby grow'?

Key Response

The STRIDER trial provides high-quality evidence that sildenafil (25 mg TID) does not prolong pregnancy or improve perinatal survival compared to placebo. Residents should counsel patients that there are currently no proven pharmacological treatments to reverse FGR. Management should focus on intensive surveillance (umbilical artery and ductus venosus Doppler) and optimized delivery timing, rather than off-label use of sildenafil which has shown no benefit and potential safety concerns in related trials.

Fellow
Fellow

The STRIDER UK trial was part of an international consortium. How do you reconcile the neutral results of this trial with the previous meta-analyses of smaller studies that suggested a potential benefit in birthweight and pregnancy prolongation?

Key Response

This illustrates the 'small study effect' and publication bias common in early-phase research. Smaller, non-blinded studies often overstate effect sizes. STRIDER, as a large, multicentre, double-blind RCT, was powered to detect a clinically meaningful difference (1 week prolongation) and found none, suggesting that the earlier observed benefits were likely due to chance, lack of rigorous blinding, or heterogeneity in the FGR phenotypes included.

Attending
Attending

STRIDER failed to show a difference in the primary outcome of pregnancy prolongation. Does this negative result signify the end of the 'angiogenic/vasodilatory' hypothesis for treating placental insufficiency, or does it point toward a failure in the timing of intervention?

Key Response

This is a critical teaching point regarding 'irreversible pathology.' By the time severe FGR is diagnosed at 22-30 weeks with abnormal Dopplers, the placental vascular architecture is often already fundamentally malformed (e.g., poor spiral artery remodeling). Sildenafil acts on vascular tone, but cannot correct structural placental defects. Future research may need to focus on first-trimester prevention (like aspirin) rather than mid-gestation rescue.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

Evaluate the choice of 'prolongation of pregnancy' as the primary endpoint in the STRIDER trial. What are the statistical risks of using a time-to-event surrogate in a population where delivery is often physician-indicated rather than spontaneous?

Key Response

In FGR trials, the duration of pregnancy is highly influenced by clinician behavior (protocolized delivery for Doppler changes) rather than just biological drug effect. This 'interventional bias' can mask a drug's true effect. A PhD researcher would argue for co-primary endpoints or a composite neonatal morbidity index that accounts for the trade-off between gaining maturity and the risk of continuing a pregnancy in a hostile intrauterine environment.

Journal Editor
Journal Editor

As a reviewer, if the STRIDER UK trial reported neutral results but a concurrent sister trial (STRIDER Holland) was stopped early for safety concerns (neonatal pulmonary hypertension), how would you ensure the manuscript's discussion properly contextualizes the risk-benefit ratio for the reader?

Key Response

An editor must ensure the paper doesn't just state 'no benefit' but also addresses 'potential harm.' Even if the UK arm didn't see a statistically significant increase in pulmonary hypertension, the discussion must integrate data from the broader consortium to prevent a 'neutral' finding from being misinterpreted as a 'safe' finding, especially when the efficacy is nil.

Guideline Committee
Guideline Committee

Given the STRIDER results, what level of recommendation should be assigned to sildenafil in clinical practice guidelines, and how does this compare to current ACOG or RCOG recommendations for FGR?

Key Response

STRIDER provides Level 1a evidence against the use of sildenafil for FGR. Current guidelines (like RCOG Green-top 31 or SMFM FGR guidelines) do not recommend sildenafil outside of research trials. Based on STRIDER, committees should issue a 'Strong Recommendation Against' its use in clinical practice, moving it from the 'experimental' category to the 'not recommended' category to prevent further off-label use that carries no benefit and potential risk.

Clinical Landscape

Noteworthy Related Trials

2018

STRIDER NZAus Trial

n = 122 · Lancet Child Adolesc Health

Tested

Sildenafil citrate 25mg three times daily

Population

Pregnant women with early-onset severe fetal growth restriction

Comparator

Placebo

Endpoint

Survival to discharge from neonatal intensive care unit

Key result: Sildenafil did not improve neonatal survival or outcomes in women with early-onset fetal growth restriction.
2018

STRIDER UK Trial

n = 135 · Lancet Child Adolesc Health

Tested

Sildenafil citrate 25mg three times daily

Population

Pregnant women with severe early-onset fetal growth restriction

Comparator

Placebo

Endpoint

Time from randomisation to birth

Key result: The study found no significant improvement in pregnancy duration or perinatal outcomes with sildenafil treatment.
2018

Dutch STRIDER Trial

n = 358 · Lancet Child Adolesc Health

Tested

Sildenafil citrate 25mg three times daily

Population

Pregnant women with severe early-onset fetal growth restriction

Comparator

Placebo

Endpoint

Perinatal mortality

Key result: Sildenafil treatment resulted in no significant reduction in perinatal mortality compared to placebo.

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