New England Journal of Medicine NOVEMBER 21, 2019

Dapagliflozin in Patients with Heart Failure and Reduced Ejection Fraction (DAPA-HF)

John J.V. McMurray, Scott D. Solomon, Silvio E. Inzucchi, Lars Køber, Mikhail N. Kosiborod, Felipe A. Martinez, Piotr Ponikowski, Marc S. Sabatine, Inder S. Anand, Jan Bělohlávek, et al.

Bottom Line

In patients with heart failure and reduced ejection fraction, the addition of dapagliflozin to standard therapy significantly reduced the risk of worsening heart failure and cardiovascular death, regardless of diabetes status.

Key Findings

1. Over a median follow-up of 18.2 months, the primary composite outcome of worsening heart failure or cardiovascular death occurred in 16.3% of the dapagliflozin group compared to 21.2% of the placebo group (HR 0.74, 95% CI 0.65-0.85; P<0.001).
2. A first worsening heart failure event was significantly reduced with dapagliflozin (10.0% vs. 13.7%; HR 0.70, 95% CI 0.59-0.83).
3. Cardiovascular death was significantly lower in the dapagliflozin arm (9.6% vs. 11.5%; HR 0.82, 95% CI 0.69-0.98).
4. All-cause mortality was reduced in patients receiving dapagliflozin compared to placebo (11.6% vs. 13.9%; HR 0.83, 95% CI 0.71-0.97).
5. The clinical benefits of dapagliflozin were highly consistent across prespecified subgroups, most notably demonstrating similar efficacy in patients with and without type 2 diabetes at baseline.

Study Design

Design
RCT
Double-Blind
Sample
4,744
Patients
Duration
18.2 mo
Median
Setting
20 countries
Population Adults with symptomatic heart failure (NYHA class II-IV), a left ventricular ejection fraction of 40% or less, and elevated NT-proBNP levels (at least 600 pg/mL, or at least 400 pg/mL if hospitalized for heart failure within 12 months), with or without type 2 diabetes.
Intervention Dapagliflozin 10 mg administered orally once daily in addition to standard guideline-directed medical therapy.
Comparator Matching placebo administered orally once daily in addition to standard guideline-directed medical therapy.
Outcome A composite of worsening heart failure (defined as an unplanned hospitalization or an urgent visit resulting in intravenous therapy for heart failure) or death from cardiovascular causes.

Study Limitations

The trial enrolled very few patients with advanced NYHA class IV heart failure (less than 1%), limiting generalizability to the most severe heart failure cases.
Black patients were underrepresented, comprising only about 5% of the study cohort.
Patients with severe chronic kidney disease (eGFR < 30 mL/min/1.73 m2) or symptomatic hypotension were excluded from the trial.
The median follow-up of 18.2 months was relatively short for evaluating long-term safety and mortality benefits.

Clinical Significance

DAPA-HF fundamentally changed the paradigm of heart failure management by proving that SGLT2 inhibitors offer profound cardiovascular and survival benefits in HFrEF independent of their glycemic effects. This landmark trial led to the rapid integration of SGLT2 inhibitors as a foundational pillar of guideline-directed medical therapy for HFrEF, alongside beta-blockers, MRAs, and ARNIs/ACE inhibitors.

Historical Context

Initially developed as an antidiabetic agent, dapagliflozin belongs to the SGLT2 inhibitor class. Prior cardiovascular outcome trials for SGLT2 inhibitors (such as EMPA-REG OUTCOME and CANVAS) unexpectedly demonstrated significant reductions in heart failure hospitalizations among patients with type 2 diabetes. DAPA-HF was designed to test whether this benefit extended to patients with established HFrEF regardless of diabetes status, successfully severing the class's exclusive therapeutic tie to diabetes management.

Guided Discussion

High-yield insights from every perspective

Med Student
Medical Student

What are the proposed physiological mechanisms by which dapagliflozin, originally developed as a glucose-lowering agent, improves outcomes in heart failure patients even in the absence of diabetes?

Key Response

SGLT2 inhibitors work via multiple non-glycemic pathways. These include osmotic diuresis and natriuresis leading to decreased preload, reduction of arterial stiffness decreasing afterload, inhibition of the myocardial Na+/H+ exchanger (NHE1), reduction in sympathetic nervous system activity, and promoting a metabolic shift toward ketone body utilization, which provides a more oxygen-efficient fuel source for the failing myocardium.

Resident
Resident

A 65-year-old non-diabetic patient with HFrEF (LVEF 35%) is currently on a beta-blocker, ARNI, and MRA, but remains symptomatic (NYHA Class II). Based on DAPA-HF, what is the rationale for adding dapagliflozin, and what specific parameters and side effects must be monitored upon initiation?

Key Response

DAPA-HF demonstrated significant reductions in CV death and HF hospitalizations regardless of diabetes status, establishing SGLT2 inhibitors as a foundational pillar of HFrEF therapy. Residents should monitor volume status, blood pressure, and renal function, anticipating a slight, benign initial 'dip' in eGFR that subsequently stabilizes. Patients must also be counseled on the risk and prevention of genital mycotic infections.

Fellow
Fellow

How does the baseline use of sacubitril/valsartan (ARNI) in the DAPA-HF trial population impact the interpretation of dapagliflozin's efficacy, and what do the subgroup analyses suggest about the simultaneous initiation of quadruple medical therapy?

Key Response

Only about 11% of patients in DAPA-HF were on an ARNI at baseline. However, subgroup analyses demonstrated that the relative risk reduction of dapagliflozin was consistent whether or not patients were taking an ARNI. This suggests additive, non-overlapping cardiovascular benefits and strongly supports the modern paradigm of rapid initiation of quadruple medical therapy rather than a historical, sequential step-up approach.

Attending
Attending

Given the profound benefits of SGLT2 inhibitors observed in DAPA-HF, how do we overcome the clinical inertia often associated with polypharmacy in HF, and how should we frame the discussion with non-diabetic patients regarding the shift from 'glycemic control' to 'cardiovascular risk modification'?

Key Response

Attendings must lead the paradigm shift by teaching that SGLT2 inhibitors are primary cardiometabolic and disease-modifying HF therapies, not just diabetes drugs. Overcoming inertia involves educating patients that this drug directly protects the heart independently of blood sugar, and streamlining initiation by preemptively adjusting loop diuretics if needed and leveraging multidisciplinary teams to ensure all HFrEF patients receive all four pillars of GDMT.

Scholarly Review

Critical appraisal through the lens of expert reviewers and guideline development

PhD
PhD

DAPA-HF utilized a composite primary endpoint of cardiovascular death, hospitalization for heart failure, or an urgent heart failure visit. From a statistical and trial design perspective, how does the inclusion of 'urgent heart failure visits' affect the trial's power, effect size estimation, and the interpretation of the proportional hazards assumption?

Key Response

Adding urgent HF visits increases the overall event rate, thereby increasing statistical power and allowing for a smaller sample size or shorter follow-up. However, it can dilute the perceived severity of the composite endpoint if the treatment primarily affects softer endpoints. Methodologists must evaluate if the treatment effect is driven solely by the least severe event (though in DAPA-HF, CV death was also independently reduced) and check for competing risks, such as non-CV death, that might violate proportional hazards assumptions over time.

Journal Editor
Journal Editor

As a peer reviewer evaluating the DAPA-HF manuscript, how would you scrutinize the handling of missing data, informative censoring, and the potential unmasking of the treatment assignment due to characteristic SGLT2 inhibitor side effects like genital mycotic infections?

Key Response

An editor would flag the risk of informative censoring if dropout rates differed between groups due to adverse events like volume depletion or acute kidney injury. Furthermore, the distinct side effect profile of SGLT2 inhibitors (e.g., genital mycotic infections or increased urination) could unmask patients and investigators to the treatment assignment, potentially biasing patient-reported outcomes or the threshold for hospital admission. Robust intention-to-treat and tipping point analyses are crucial to validate the findings against these threats.

Guideline Committee
Guideline Committee

Following the publication of DAPA-HF and EMPEROR-Reduced, how should heart failure guidelines be updated regarding the classification and sequencing of SGLT2 inhibitors for HFrEF, and what Level of Evidence and Class of Recommendation should be assigned compared to historical standard therapies?

Key Response

DAPA-HF provided pivotal evidence that led to a Class 1, Level of Evidence A recommendation in the 2022 AHA/ACC/HFSA guidelines for SGLT2 inhibitors in symptomatic chronic HFrEF to reduce hospitalization and CV mortality, irrespective of diabetes status. The committee must emphasize that SGLT2 inhibitors should be considered foundational, first-line agents alongside beta-blockers, MRAs, and ARNIs, officially transitioning the guidelines from a tiered, sequential approach to a simultaneous or rapid-sequence quadruple therapy strategy.

Clinical Landscape

Noteworthy Related Trials

2014

PARADIGM-HF

n = 8,399 · NEJM

Tested

Sacubitril/valsartan 200mg twice daily

Population

Patients with heart failure and reduced ejection fraction (HFrEF)

Comparator

Enalapril 10mg twice daily

Endpoint

Composite of cardiovascular death or hospitalization for heart failure

Key result: Sacubitril/valsartan was superior to enalapril in significantly reducing the risks of cardiovascular death and hospitalization for heart failure.
2015

EMPA-REG OUTCOME

n = 7,020 · NEJM

Tested

Empagliflozin 10mg or 25mg daily

Population

Patients with type 2 diabetes and established cardiovascular disease

Comparator

Placebo

Endpoint

3-point MACE (CV death, nonfatal MI, nonfatal stroke)

Key result: Empagliflozin significantly reduced the risk of 3-point MACE, cardiovascular death, and notably reduced hospitalizations for heart failure by 35 percent.
2020

EMPEROR-Reduced

n = 3,730 · NEJM

Tested

Empagliflozin 10mg daily

Population

Patients with heart failure and reduced ejection fraction (HFrEF)

Comparator

Placebo

Endpoint

Composite of cardiovascular death or hospitalization for heart failure

Key result: Empagliflozin significantly reduced the risk of cardiovascular death or hospitalization for heart failure by 25 percent compared to placebo.

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